8
Participants
Start Date
March 10, 2017
Primary Completion Date
January 23, 2019
Study Completion Date
January 23, 2019
Children's Hospital at Montefiore, The Bronx
Clinic for Special Children, Strasburg
Shaare Zedek Medical Center, Jerusalem
King's College Hospital, London
Lead Sponsor
Audentes Therapeutics
INDUSTRY