139
Participants
Start Date
March 8, 2017
Primary Completion Date
August 12, 2024
Study Completion Date
August 12, 2024
Tofersen
Participants will receive a loading dose regimen followed by maintenance dosing.
Bispebjerg Hospital, Copenhagen
Research Site, Leuven
Research Site, Torino
Research Site, Baltimore
Research Site, Atlanta
Research Site, Jacksonville
Research Site, Orlando
Research Site, Miami
Research Site, Knoxville
Research Site, Cleveland
Research Site, Rochester
Research Site, Chicago
Research Site, Clermont-Ferrand
Research Site, St Louis
Research Site, Lincoln
Research Site, Phoenix
Research Site, Ulm
Research Site, San Francisco
Research Site, Portland
Research Site, La Jolla
Research Site, Boston
Research Site, Calgary
Research Site, Edmonton
Research Site, Toronto
Research Site, Montreal
Research Site, Bunkyō City
Research Site, Kagoshima
Research Site, Shinjuku-ku
Research Site, Suita-shi
Research Site, Sheffield
Lead Sponsor
Collaborators (1)
Ionis Pharmaceuticals, Inc.
INDUSTRY
Biogen
INDUSTRY