Trial Readiness and Endpoint Assessment in Congenital Myotonic Dystrophy

CompletedOBSERVATIONAL

Enrollment

100

Participants

Timeline

Start Date

December 14, 2016

Primary Completion Date

December 8, 2021

Study Completion Date

January 27, 2025

Conditions

Congenital Myotonic Dystrophy

Interventions

OTHER

Natural history

Longitudinal disease progression

Trial Locations (3)

Centro Clinico Nemo, Milan

Virginia Commonwealth University, Richmond

Pediatric Neuromuscular Research, Children's Hospital - LHSC, London

All Listed Sponsors

collaborator

Fondazione Serena Onlus - Centro Clinico NeMO Milano

OTHER

collaborator

University of Western Ontario, Canada, Children's Health Research Institute

UNKNOWN

lead

Virginia Commonwealth University

OTHER

NCT03059264 - Trial Readiness and Endpoint Assessment in Congenital Myotonic Dystrophy | Biotech Hunter | Biotech Hunter