166
Participants
Start Date
July 6, 2017
Primary Completion Date
April 28, 2020
Study Completion Date
April 28, 2020
RO7239361
Take RO7239361 subcutaneously on specified days over a 48 week blinded period
Placebo for RO7239361
Take placebo subcutaneously on specified days over a 48 week blinded period
Children's Hospital Westmead; Paediatrics & Child Health, Westmead
Royal Children's Hospital, Parkville
Lady Cilento Children's Hospital; Neurosciences Department, South Brisbane
UZ Gent, Ghent
Fondazione Serena Onlus - CENTRO CLINICO NEMO, Milano
Kennedy Krieger Institute, Baltimore
Rare Disease Research, LLC, Atlanta
University of Florida, Gainesville
Nemours Children's Hospital, Orlando
Drottning Silvias Barn- och ungdomssjukhus; Kliniken for barnmedicin, Gothenburg
Nationwide Childrens Hospital; Research Institute at Nationwide Childrens Hospital, Columbus
Hotel Dieu; Service Pharmacie Essais Cliniques, Nantes
Universitatsklinikum Essen; Innere Klinik, Essen
Cincinnati Childrens Hospital Medical Center;Investigational Pharmacy, Cincinnati
Hospital Universitari i Politecnic La Fe de Valencia; Servicio de Farmacia, Valencia
University of Iowa, Iowa City
Rush University Medical Center - PPDS, Chicago
Saint Louis Children's Hospital, St Louis
University of Kansas Medical Center, Kansas City
Hopitaux Universitaires de Strasbourg, Strasbourg
Hospices Civils de Lyon, Lyon
Hopital Armand Trousseau; centre reference Maladies Neuro-musculaires Est parisien Neuropediatrie, Paris
Neuromuscular Research Center, Phoenix
Las Vegas Clinic, Las Vegas
Stanford University, Palo Alto
University of California Davis Medical Center, Sacramento
Seattle Children's Hospital, Seattle
Az. Osp. Universitaria Pol. G. Martino; Dip. Neuroscienze, Scienze Psichiatriche e Anest., Messina
Yale University School of Medicine ; Pulmonary & Critical Care, New Haven
University of Massachusetts Memorial Childrens Medical Center; Department of Neurology, Worcester
Instituto centenario, Buenos Aires
London Health Sciences Centre; Children's Hospital; Pediatrics, London
Children'S Hospital of Eastern Ontario, Ottawa
Fondazione Policlinico Universitario A Gemelli; Servizio di Farmacia, Rome
Hyogo College of Medicine Hospital, Hyōgo
Miyagi Children's Hospital, Miyagi
Shinshu University Hospital, Nagano
National Hospital Organization Osaka Toneyama Medical Center, Osaka
National Center of Neurology and Psychiatry, Tokyo
Leids Universitair Medisch Centrum, Leiden
Radboud University Nijmegen Medical Centre; Ophthalmology, Nijmegen
Hospital Sant Joan De Deu, Esplugues de Llobregas
Alder Hey Children s Hospital; Department of Pediatrics, Liverpool
UCL Institute of Child Health & Great Ormond Street Hospital for Children, London
Hoffmann-La Roche
INDUSTRY