174
Participants
Start Date
March 3, 2017
Primary Completion Date
February 7, 2025
Study Completion Date
February 7, 2025
Risdiplam
Risdiplam will be administered orally once daily.
UZ Leuven Gasthuisberg, Leuven
Universitäts-Kinderspital (UKBB) Neuropädiatrie, Basel
UZ Gent, Ghent
Columbia University Medical Center, New York
IRCCS Istituto Giannina Gaslini, Genoa
Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan
Hopital des Enfants, Toulouse
Nemours Children's Hospital, Orlando
CHRU de Montpellier, Hopital Gui de Chauliac, Montpellier
Universitätsklinikum Essen, Essen
Hopital Roger Salengro, Lille
Hopital Femme Mere Enfant, Bron
Hôpital Necker-Enfants Malades, Paris
Universitätsklinikum Freiburg, Freiburg im Breisgau
Stanford University Medical Center, Palo Alto
UOSD Malattie Neurodegenerative, Messina
Boston Childrens Hospital, Boston
IRCCS Ospedale Pediatrico Bambino Gesù, Rome
Policlinico Agostino Gemelli, Rome
UMC Utrecht, Utrecht
Klinika Neurologii I Wydzialu Lekarskiego WUM w Warszawie, Warsaw
Birmingham Heartlands Hospital, Birmingham
UCL Institute of Child Health & Great Ormond Street Hospital for Children, London
The Newcastle upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne
Hoffmann-La Roche
INDUSTRY