A Cross-specialty Collaboration Platform for Mucopolysaccharidosis Confirmative Diagnosis

UnknownOBSERVATIONAL
Enrollment

100

Participants

Timeline

Start Date

January 1, 2018

Primary Completion Date

December 31, 2020

Study Completion Date

December 31, 2020

Conditions
Mucopolysaccharidoses
Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

BioMarin Pharmaceutical

INDUSTRY

lead

Mackay Memorial Hospital

OTHER