25
Participants
Start Date
January 26, 2017
Primary Completion Date
December 5, 2023
Study Completion Date
December 5, 2023
SPK-8011
A novel, bio-engineered, recombinant adeno-associated viral vector carrying human factor VIII gene
Royal Prince Alfred Hosptial, Camperdown
The Alfred Hospital, Melbourne
Weill Cornell Medicine-Comprehensive Center for Hemophilia and Coagulation Disorders, New York
Mahidol University - Ramathibody Hospital, Bangkok
Pennsylvania State University Milton S. Hershey Medical Center, Hershey
Hemophilia Center of Western Pennsylvania, Pittsburgh
Children's Hospital of Philadelphia, Philadelphia
Jefferson University Hospitals, Philadelphia
Virginia Commonwealth University School of Medicine, Richmond
University of Florida Health, Gainesville
Mississippi Center for Advanced Medicine, Madison
University of California Davis - Hemostasis and Thrombosis Center, Sacramento
Oregon Health & Science University, Portland
Chaim Sheba Center, Ramat Gan
Boston Children's Hospital, Boston
McMaster University Medical Centre and Juravinski Hospital, Hamilton
Spark Therapeutics, Inc.
INDUSTRY