Natural History Study of Homocystinuria Caused by Cystathionine Beta-Synthase Deficiency (ACAPPELLA)

RecruitingOBSERVATIONAL
Enrollment

150

Participants

Timeline

Start Date

January 31, 2017

Primary Completion Date

April 30, 2026

Study Completion Date

August 31, 2026

Conditions
Homocystinuria Due to CBS Deficiency
Trial Locations (11)

1

RECRUITING

Travere Investigational Site, Dublin

19104

RECRUITING

Travere Investigational Site (Enrolling 1 to <5 Year-olds Only), Philadelphia

20010

RECRUITING

Travere Investigational Site (Enrolling 1 to <5 Year-olds Only), Washington D.C.

30322

COMPLETED

Travere Investigational Site, Atlanta

46202

COMPLETED

Travere Investigational Site, Indianapolis

80045

RECRUITING

Travere Investigational Site (Enrolling 1 to <5 Year-olds Only), Aurora

90230

COMPLETED

Travere Investigational Site - Virtual Site, Culver City

02115

COMPLETED

Travere Investigational Site, Boston

Unknown

RECRUITING

Travere Investigational Site, Doha

RECRUITING

Travere Investigational Site, Doha

M6 8HD

COMPLETED

Travere Investigational Site, Salford

All Listed Sponsors
lead

Travere Therapeutics, Inc.

INDUSTRY