60
Participants
Start Date
September 30, 2014
Primary Completion Date
September 30, 2026
Study Completion Date
September 30, 2026
RECRUITING
State University of New York at Buffalo, Buffalo
Rare Diseases Clinical Research Network
NETWORK
National Center for Advancing Translational Sciences (NCATS)
NIH
Lysosomal Disease Network
OTHER
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
NIH
State University of New York at Buffalo
OTHER