Phase 3 Randomized, Open-Label Study of Guadecitabine vs Treatment Choice in Previously Treated Acute Myeloid Leukemia

PHASE3CompletedINTERVENTIONAL
Enrollment

302

Participants

Timeline

Start Date

March 16, 2017

Primary Completion Date

January 20, 2020

Study Completion Date

June 1, 2020

Conditions
Acute Myeloid Leukemia
Interventions
DRUG

guadecitabine

In Cycle 1, guadecitabine will be given for 10 days on Days 1-5 and Days 8-12. In Cycle 2, the guadecitabine dose will be 60 mg/m\^2 for either 10 days (Days 1-5 and 8-12) or 5 days (Days 1-5 only) based on assessment of disease response, and hematological recovery by Day ≥28.

DRUG

Treatment Choice (TC)

"* High intensity: intermediate or high dose cytarabine (HiDAC); mitoxantrone, etoposide, and cytarabine (MEC); or fludarabine, cytarabine, G-CSF, +/- idarubicin (FLAG/FLAG-Ida).~* Low intensity: low dose cytarabine (LDAC), decitabine, or azacitidine.~* Best Supportive Care (BSC)."

Trial Locations (95)

1083

SE ÁOK I. sz. Belgyógyászati Klinika, Budapest

1200

Cliniques Universitaires Saint-Luc, Brussels

2100

Rigshospitalet, Copenhagen

3080

Seoul National University Hospital, Seoul

3722

Severance Hospital, Seoul

4032

Debreceni Egyetem Klinikai Központ, Debrecen

4103

Universitätsklinikum Leipzig, Leipzig

5505

Asan Medical Center, Seoul

6120

Universitätsklinikum Halle (Saale), Halle

6351

Samsung Medical Center, Seoul

6591

The Catholic University of Korea, Seoul St. Mary's Hospital, Seoul

6725

Szegedi Tudományegyetem, Szeged

7400

Somogy Megyei Kaposi Mór Oktató Kórház, Kaposvár

8000

AZ Sint-Jan Brugge-Oostende AV, Bruges

Aarhus University Hospital, Aarhus C

8036

Hospital Clínic de Barcelona, Barcelona

8041

Hospital de la Santa Creu i Sant Pau, Barcelona

8907

Hospital Duran i Reynals, Barcelona

9000

Universitair Ziekenhuis Gent, Ghent

10003

Hospital San Pedro de Alcántara, Cáceres

10021

Weill Cornell Medical College, New York

13385

Hôpital de la Conception, Marseille

14004

Hospital Universitario Reina Sofía, Córdoba

14263

Roswell Park Cancer Institute, Buffalo

16132

IRCCS AOU San Martino - IST, Genova

19104

Hospital of the University of Pennsylvania, Philadelphia

20122

Fondazione IRCCS Cà Granda Ospedale Maggiore Policlinico, Milan

20132

Ospedale San Raffaele - Milano, Milan

24105

Universitätsklinikum Schleswig-Holstein, Kiel

26506

West Virginia University Hospitals, Inc., Morgantown

27710

Duke Cancer Institute, Durham

28007

Hospital General Universitario Gregorio Marañón, Madrid

29000

Khmelnytskyi Regional Hospital, Khmelnytskyi

31059

Institut Universitaire du Cancer de Toulouse - Oncopole, Toulouse

33011

Hospital Universitario Central de Asturias, Oviedo

33100

A.S.U Integrata di Udine - Presidio Ospedaliero Santa Maria della Misericordia, Udine

33604

CHU Hopitaux de Bordeaux - Hôpital Haut-Lévêque, Pessac

34295

CHRU Montpellier - Saint Eloi, Montpellier

36011

Poltava Regional Clinical Hospital named after M. V. Sklifosovskoho, Poltava

37232

Vanderbilt University Medical Center, Nashville

38114

Städtisches Klinikum Braunschweig gGmbH, Braunschweig

40479

Marien Hospital Düsseldorf GmbH, Düsseldorf

41013

Hospital Universitario Virgen del Rocío, Seville

44033

Ulsan University Hospital (UUH), Ulsan

46017

Hospital Universitario Dr. Peset, Valencia

46026

Hospital Universitari i Politècnic La Fe, Valencia

46237

Franciscan Research Center, Indianapolis

49241

Pusan National University Hospital, Busan

60637

The University of Chicago Medical Center, Chicago

64100

Centre Hospitalier de la Côte Basque, Bayonne

68100

Groupe Hospitalier de la Région de Mulhouse et Sud Alsace, Mulhouse

69310

Centre Hospitalier Lyon-Sud, Pierre-Bénite

75246

Baylor Research Institute, Dallas

75475

Hôpital Saint-Louis, Paris

76038

Centre Henri Becquerel, Rouen

77030

MD Anderson Cancer Center, Houston

80131

"A.O.R.N. A. Cardarelli", Napoli

81377

Klinikum der Universität München, München

87106

University of New Mexico School of Medicine, Albuquerque

89081

Universitätsklinikum Ulm, Ulm

90033

University of Southern California, Los Angeles

07601-1915

John Theurer Cancer Center at Hackensack University Medical Center, Hackensack

73104-5418

University of Oklahoma Medical Center, Oklahoma City

19111-2433

Temple University Hospital, Philadelphia

T2N 4N2

Tom Baker Cancer Centre, Calgary

T6G 2V2

University of Alberta Hospital, Edmonton

M5G 2C1

Princess Margaret Cancer Centre, Toronto

H4A 3J1

McGill University Health Centre, Montreal

H1T 2M4

Hopital Maisonneuve Rosemont, Montreal

Unknown

Medizinischen Fakultät Mannheim der Universität Heidelberg, Mannheim

Pecsi Tudomanyegyetem Klinikai Központ, Pécs

Vall d'Hebron Institut d'Oncologia, Barcelona

010-8543

Akita University Hospital, Akita

720-0001

Chugoku Central Hospital, Fukuyama-Shi

259-1193

Tokai University Hospital, Isehara-shi

350-8550

Saitama Medical Center, Kawagoe-Shi

650-0047

Kobe City Medical Center General Hospital, Kobe

602-8026

Japanese Red Cross Kyoto Daini Hospital, Kyoto

602-8566

University Hospital, Kyoto Prefectural University of Medicine, Kyoto

371-0821

Gunmaken Saiseikai Maebashi Hospital, Maebashi

852-8501

Nagasaki University Hospital, Nagasaki

852-8511

The Japanese Red Cross Nagasaki Genbaku Hospital, Nagasaki

589-8511

Kindai University Hospital, Osakasayama-Shi

849-8501

Saga University Hospital, Saga

141-8625

NTT Medical Center Tokyo, Shinagawa-Ku

411-8777

Shizuoka Cancer Center, Shizuoka

190-0014

National Hospital Organization Disaster Medical Center, Tachikawa-Shi

990-9585

Yamagata University Hospital, Yamagata

910-1193

University of Fukui Hospital, Yoshida-Gun

02-776

Instytut Hematologii i Transfuzjologi, Warsaw

413 45

Sahlgrenska University Hospital, Gothenburg

B9 5SS

Heart of England NHS Foundation Trust - Heartlands Hospital, Birmingham

BS2 8ED

University Hospitals Bristol NHS Foundation Trust - Bristol Haematology and Oncology Centre, Bristol

CT1 3NG

East Kent Hospitals University NHS Foundation Trust - Kent and Canterbury Hospital, Canterbury

LS9 7TF

St. James's University Hospital, Leeds

Sponsors
All Listed Sponsors
lead

Astex Pharmaceuticals, Inc.

INDUSTRY