Triheptanoin in Mc Ardle

PHASE2CompletedINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

November 16, 2016

Primary Completion Date

June 26, 2017

Study Completion Date

June 26, 2017

Conditions
Glycogen Storage Disease Type V
Interventions
DRUG

Triheptanoin

Anaplerotic dietary oil

DRUG

Placebo oil

Safflower oil

Trial Locations (1)

75651

Pitié-Salpêtrière,centre de référence de pathologie neuromusculaire, 47 Bd de l'hôpital, Paris

All Listed Sponsors
collaborator

Rigshospitalet, Denmark

OTHER

lead

Institut National de la Santé Et de la Recherche Médicale, France

OTHER_GOV

NCT02919631 - Triheptanoin in Mc Ardle | Biotech Hunter | Biotech Hunter