Investigate Safety, Tolerability, PK, PD and Efficacy of Risdiplam (RO7034067) in Infants With Type1 Spinal Muscular Atrophy

UZ Leuven Gasthuisberg, Leuven

Chr de La Citadelle, Liège

Universitäts-Kinderspital (UKBB) Neuropädiatrie, Basel

UZ Gent, Ghent

Clinical Medical Center Zagreb; University Hospital Rebro Department of Paediatrics, Zagreb

Columbia University Medical Center; The Neurological Institute of New York, New York

Institute for Mother and Child Dr. Vukan Cupic, Belgrade

King Faisal Specialist Hospital and Research Centre Building, Riyadh

IRCCS Istituto Giannina Gaslini; U.O.S.D. Centro di Miologia e Patologie Neurodegenerative, Genoa

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico; Unità Operativa Complessa di Neurologia, Milan

Fondazione IRCCS Istituto Neurologico ?Carlo Besta?; UO di Neurologia dello Sviluppo, Milan

Hospital Yeditepe University Kozyatagi; Pediatry, Atasehir- Istanbul

Hospital Universitario Virgen del Rocio, Seville

Ann and Robert H. Lurie Children Hospital of Chicago, Chicago

Ams of Ukraine; Inst. of Neurology, Psychiatry & Narcology, Kharkiv

Hopital Femme Mere Enfant; Medecine Physique et Readaptation Pediatrique ? L?ESCALE, Bron

Hopital Armand Trousseau, Paris

Stanford University Medical Center, Palo Alto

Peking University First Hospital, Beijing

Russian Children Neuromuscular Center of Veltischev, Moscow

Children's Hospital of Fudan University, Shanghai

Boston Childrens Hospital, Boston

Instituto de Puericultura E Pediatria Martagão Gesteira, Rio de Janeiro

Hospital das Clinicas - FMUSP_X; Neurologia, São Paulo

IRCCS Ospedale Pediatrico Bambino Gesù; U.O. Malattie Neuromuscolari e Neurodegenerative, Rome

Policlinico Agostino Gemelli; Dipartimento di Neuropsichiatria Infantile, Rome

Hyogo Medical University Hospital, Hyōgo

Szpital Gdanskiego Uniwersytetu Medycznego; Clinic of developmental neurology, Gda?sk

The Children?s Memorial Health Institute Department of Neurology and Epileptology, Warsaw

Hospital Sant Joan De Deu, Esplugues de Llobregas

Hospital Universitari Vall d'Hebron; Area Genética Clínica y Molecular, Barcelona

Hacettepe University, School of Medicine; Pediatrics Department; Pediatrics Child Neurology Unit, Ankara