A Study to Investigate the Safety, Tolerability, Pharmacokinetics, Pharmacodynamics and Efficacy of Risdiplam (RO7034067) in Type 2 and 3 Spinal Muscular Atrophy (SMA) Participants

UZ Leuven Gasthuisberg, Leuven

Chr de La Citadelle, Liège

UZ Gent, Ghent

Clinical Medical Center Zagreb; University Hospital Rebro Department of Paediatrics, Zagreb

Columbia University Medical Center; The Neurological Institute of New York, New York

Clinic for Neurology and Psychiatry for Children and Youth, Belgrade

IRCCS Istituto Giannina Gaslini; U.O.S.D. Centro di Miologia e Patologie Neurodegenerative, Genoa

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico; Unità Operativa Complessa di Neurologia, Milan

Fondazione IRCCS Istituto Neurologico ?Carlo Besta?; UO di Neurologia dello Sviluppo, Milan

Hospital Yeditepe University Kozyatagi; Pediatry, Atasehir- Istanbul

Hospital Universitario Virgen del Rocío, Seville

CHU de Nantes - Hotel Dieu, Nantes

Hopital Roger Salengro, Lille

Hopital Femme Mere Enfant; Medecine Physique et Readaptation Pediatrique ? L?ESCALE, Bron

Hôpital Necker-Enfants Malades; Service de neuropédiatrie, Paris

Hopital Armand Trousseau, Paris

Universitätsklinikum Freiburg; Klinik für Neuropädiatrie und Muskelerkrankungen, Freiburg im Breisgau

Stanford University Medical Center, Palo Alto

Peking University First Hospital, Beijing

Russian Children Neuromuscular Center of Veltischev, Moscow

Children's Hospital of Fudan University, Shanghai

Hospital Universitario La Paz, Madrid

Instituto de Puericultura E Pediatria Martagão Gesteira, Rio de Janeiro

Alberta Children's Hospital Division of Pediatric Neurology, Calgary

London Health Sciences Centre; Children's Hospital; Pediatrics, London

McGill University Health Centre - Glen Site, Montreal

IRCCS Ospedale Pediatrico Bambino Gesù; U.O. Malattie Neuromuscolari e Neurodegenerative, Rome

Policlinico Agostino Gemelli; Dipartimento di Neuropsichiatria Infantile, Rome

Fukuoka Children's Hospital, Fukuoka

Hiroshima University Hospital, Hiroshima

Hyogo Medical University Hospital, Hyōgo

Minami Kyushu National Hospital, Kagoshima

Miyagi Children's Hospital, Miyagi

Shiga Medical Center for Children, Shiga

Shizuoka Children's Hospital, Shizuoka

Jichi Medical University Hospital, Tochigi

Center Hospital of the National Center for Global Health and Medicine, Tokyo

National Center Of Neurology And Psychiatry Hospital, Tokyo

Szpital Gdanskiego Uniwersytetu Medycznego; Clinic of developmental neurology, Gda?sk

Uniwersytecki Szpital Kliniczny w Poznaniu; Od. Kliniczny Neurologii Dzieci i M?odziezy, Późna

Klinika Neurologii I Wydzialu Lekarskiego WUM w Warszawie, Warsaw

Hospital Sant Joan De Deu, Esplugues de Llobregas

Hospital Universitari Vall d'Hebron; Servicio de Reumatologia, Barcelona

Hacettepe University, School of Medicine; Pediatrics Department; Pediatrics Child Neurology Unit, Ankara

University of Oxford; Department of Paediatrics, Headington