Guadecitabine (SGI-110) vs Treatment Choice in Adults With MDS or CMML Previously Treated With HMAs

PHASE3CompletedINTERVENTIONAL
Enrollment

417

Participants

Timeline

Start Date

January 13, 2017

Primary Completion Date

March 31, 2020

Study Completion Date

November 30, 2020

Conditions
Myelodysplastic SyndromesLeukemia, Myelomonocytic, Chronic
Interventions
DRUG

Guadecitabine

OTHER

Treatment Choice

"* BSC: according to standard/institutional practice; included RBC or platelet transfusions; growth factors, i.e. erythropoiesis stimulating agents, granulocyte stimulating factors, iron chelating therapy; broad spectrum antibiotics and/or antifungals.~* LDAC: 20 mg/m\^2 SC or IV once daily (QD) for 14 days in 28-day cycles. Other schedules were allowed per institutional practice. Treatment for ≥4 cycles absent disease progression/toxicity. BSC per institutional/standard practice.~* Standard Intensive Chemotherapy: recommended regimen of 7+3 was given as cytarabine 100-200 mg/m\^2/day continuous infusion for 7 days and an anthracycline for 3 days. Anthracyclines per institutional practice included daunorubicin (45-60 mg/m\^2/day) or idarubicin (9-12 mg/m\^2/day) or mitoxantrone (8-12 mg/m\^2/day) by IV infusion. Participants with complete or partial response after IC induction received ≥1 additional cycles with reduced cytotoxic doses then BSC per standard /institutional practice."

Trial Locations (112)

10065

Weill Cornell Medical College, New York

11794

Stony Brook University Medical Center, Stony Brook

14263

Roswell Park Cancer Institute, Buffalo

17033

Penn State Milton S. Hershey Medical Center, Hershey

19111

Fox Chase Cancer Center, Philadelphia

21201

University of Maryland, Baltimore

26506

West Virginia University Mary Babb Randolph Cancer Center, Morgantown

27705

Duke Cancer Center, Durham

29425

Medical University of South Carolina, Charleston

29607

Bon Secours Saint Francis Hospital, Greenville

32003

Cancer Specialists of North Florida, Fleming Island

33140

Mount Sinai Medical Center, Miami Beach

44033

Ulsan University Hospital, Ulsan

46237

Franciscan Health Indianapolis, Indianapolis

48109

University of Michigan Cancer Center, Ann Arbor

60201

North Shore Medical Center, Evanston

60612

Rush University Medical Center, Chicago

77030

University of Texas MD Anderson Cancer Center, Houston

91010

City of Hope, Duarte

92270

Desert Hematology Oncology Medical Group, Inc., Rancho Mirage

98104

Swedish Cancer Institute, Seattle

98109

Fred Hutchinson Cancer Research Center, Seattle

07601

John Theurer Cancer Center, Hackensack

Unknown

Ziekenhuis Netwerk Antwerpen Stuivenberg, Antwerp

Algemeen Ziekenhuis Sint-Jan Brugge-Oostende, Bruges

Grand Hôpital de Charleroi - Notre Dame, Charleroi

Burnaby Hospital, Burnaby

Moncton Hospital, Moncton

Maisonneuve-Rosemont Hôpital Service d'Hematologie et d'Oncologie Medicale, Montreal

Saskatchewan Cancer Agency, Regina

Fakultní nemocnice Brno, Brno

Fakultni Nemocnice Hradec Králové, Hradec Králové

Fakultní nemocnice Ostrava, Ostrava

Fakultní Nemocnice Královské Vinohrady, Prague

Onkologická klinika Všeobecná fakultní nemocnice v Praze a 1, Prague

Aalborg Universitetshospital, Aalborg

Aarhus Universitetshospital, Aarhus

Rigshospitalet, Copenhagen

Odense University Hospital, Odense

Centre Hospitalier Universitaire, La Tronche

Hôpital Dupuytren, Limoges

GHR Mulhouse Sud-Alsace, Mulhouse

Hôpital Hôtel-Dieu, Nantes

Centre Antoine Lacassagne, Nice

Hôpital Saint Louis, Paris

Centre Hospitalier Lyon Sud, Pierre-Bénite

Centre Hospitalier Universitaire de Toulouse, Toulouse

Städtisches Klinikum Braunschweig, Braunschweig

Marien Hospital Düsseldorf, Düsseldorf

Universitaetsklinikum Freiburg, Freiburg im Breisgau

Universitätsklinikum Halle, Halle

Universitätsklinikum Ulm, Ulm

Azienda Ospedaliera SS. Antonio E. Biagio E. Cesare Arrigo di Alessandria, Alessandria

Azienda Ospedaliero Universitaria Careggi, Florence

Azienda Ospedaliera Universitaria San Martino, Genova

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico, Milan

AORN A. Cardarelli, Napoli

Azienda Ospedaliera Universitaria-Maggiore della Carità di Novara, Novara

Azienda Ospedaliera Ospedali Riuniti Marche Nord, Pesaro

Ospedale S. Eugenio, Roma

NHO Nagoya Medical Center, Nagoya

Narita Red Cross Hospital, Narita

University of Fukui Hospital, Yoshida

Chugoku Central Hospital, Fukuyama-shi

Tokai University Hospital, Isehara

Kitasato University Hospital, Sagamihara-shi

Yokohama Municipal Citizen's Hospital, Yokohama

Nagasaki University Hospital, Nagasaki

Kansai Medical University Hirakata, Hirakata

Kindai University Hospital, Osakasayama-shi

Saitama Medical Center, Kawagoe

Nippon Medical School Hospital, Bunkyō-Ku

The Cancer Institute Hospital of Japanese Foundation for Cancer Research, Koto

NTT Medical Center Tokyo, Shinagawa

National Hospital Organization Disaster Medical Center, Tachikawa

National Hospital Organization Kyushu, Fukuoka

Fukushima Medical University, Fukushima

Gifu Municipal Hospital, Gifu

National Hospital Organization Kumamoto Medical Center, Kumamoto

Japanese Red Cross Kyoto Daini Hospital, Kyoto

University Hospital-Kyoto Prefectural University of Medicine, Kyoto

Yamagata University Hospital, Yamagata

Samodzielny Publiczny Szpital Kliniczny nr 1 w Lublinie, Lublin

Instytut Hematologii i Transfuzjologii, Warsaw

Samodzielny Publiczny Centralny Szpital Kliniczny, Warsaw

Hospital General Universitario de Alicante, Alicante

Hospital Universitari Germans Trias i Pujol, Badalona

Fundació Hospital de la Santa Creu i Sant Pau, Barcelona

Hospital Universitario Vall d'Hebron, Barcelona

Hospital San Pedro de Alcantara, Cáceres

Hospital de León, León

Hospital General Universitario Gregorio Marañon, Madrid

Hospital Universitario 12 de Octubre, Madrid

Hospital Universitario Ramón Y Cajal, Madrid

Hospital Universitario de Salamanca, Salamanca

Hospital Universitari i Politecnic La Fe de Valencia, Valencia

Sahlgrenska Universitetssjukhuset, Östra sjukhuset, Gothenburg

Universitetssjukhuset Örebro, Örebro

Medway NHS Foundation Trust, Gillingham

The Leeds Teaching Hospitals NHS Trust, Leeds

Chelsea and Westminster Hospital NHS Foundation Trust, London

Nottingham University Hospitals NHS Trust, Nottingham

T2N 4N2

Tom Baker Cancer Center, Calgary

T6G 2B7

University of Alberta Hospital, Edmonton

L4M 6M2

Royal Victoria Regional Health Centre, Barrie

L8V 1C3

Juravinski Cancer Centre, Hamilton

M5G 2C1

Princess Margaret Hospital, Toronto

03080

Seoul National University Hospital, Seoul

03722

Severance Hospital, Yonsei University Health System, Seoul

05505

Asan Medical Center, Seoul

06351

Samsung Medical Center, Seoul

137-701

Seoul Saint Mary's Hospital, Seoul

Sponsors
All Listed Sponsors
lead

Astex Pharmaceuticals, Inc.

INDUSTRY