112
Participants
Start Date
June 1, 2016
Primary Completion Date
December 31, 2019
Study Completion Date
December 31, 2020
glucosidase alfa
Long-term use in an observational study of licenced drug
Friedrich-Baur-Institute, Dep. of Neurology Klinikum der Universitaet Muenchen Munich, Germany, Munich
5. Department of Clinical and Experimental Medicine, Reference Center for Rare Neuromuscular Disorders, University of Messina, Italy, Messina
National Taiwan University Hospital Taipei, Taipei
Genzyme, a Sanofi Company
INDUSTRY
LMU Klinikum
OTHER