Natural History Study of Patients With MPS IIIA

CompletedOBSERVATIONAL
Enrollment

23

Participants

Timeline

Start Date

April 30, 2016

Primary Completion Date

May 31, 2019

Study Completion Date

May 31, 2019

Conditions
Mucopolysaccharidosis IIIA
Trial Locations (5)

90035-003

Hospital de Clinicas de Porto Alegre, Porto Alegre

Unknown

Armand Trousseau Public Hospital, Paris

University Medical Center Hamburg-Eppendorf, Hamburg

Academic Medical Center, Emma Children's Hospital, Amsterdam

Great Ormond Street Hospital NHS Foundation Trust, London

Sponsors

Lead Sponsor

All Listed Sponsors
lead

LYSOGENE

INDUSTRY