1,044
Participants
Start Date
November 30, 2015
Primary Completion Date
July 31, 2021
Study Completion Date
July 31, 2021
Greenwood Genetic Center, Greenwood
University of Alabama at Birmingham, Birmingham
Vanderbilt University, Nashville
Cleveland Clinic, Cleveland
Cincinnati Children's Hospital Medical Center, Cincinnati
Gillette Children's Specialty Healthcare, Saint Paul
Rush University Medical Center, Chicago
Baylor College of Medicine, Houston
University of California San Diego, San Diego
UCSF Oakland Benioff Children's Hospital, Oakland
University of Colorado Denver, Denver
Children's Hospital Boston, Boston
Washington University School of Medicine and St. Louis Children's Hospital, St Louis
Children's Hospital of Philadelphia, Philadelphia
National Institutes of Health (NIH)
NIH
National Center for Advancing Translational Sciences (NCATS)
NIH
Rare Diseases Clinical Research Network
NETWORK
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
NIH
National Institute of Neurological Disorders and Stroke (NINDS)
NIH
University of Alabama at Birmingham
OTHER