Study Assessing PTI-428 Safety, Tolerability, and Pharmacokinetics in Subjects With Cystic Fibrosis

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

56

Participants

Timeline

Start Date

July 19, 2016

Primary Completion Date

November 28, 2017

Study Completion Date

November 28, 2017

Conditions
Cystic Fibrosis
Interventions
DRUG

PTI-428

DRUG

Placebo

Trial Locations (29)

2100

University of Copenhagen Rigshospitalet, Copenhagen

10117

Charite - Campus Virchow-Klinikum, Berlin

17033

Penn State Milton S. Hershey Medical Center, Hershey

19107

Drexel University College of Medicine, Philadelphia

27710

Duke University Health System, Durham

29425

Medical University of South Carolina, Charleston

32610

University of Florida College of Medicine, Gainesville

32803

Central Florida Pulmonary Group, Altamonte Springs

33076

Groupe Hospitalier Pellegrin - Hôpital des Enfants, Bordeaux

37232

Vanderbilt University Medical Center, Nashville

40202

University of Louisville, Louisville

48109

Universiy of Michigan Health System, Ann Arbor

52242

University of Iowa, Iowa City

55905

Mayo Clinic, Rochester

60590

Universitaetsklinikum Frankfurt-Zentrum der Inneren Medizin, Frankfurt

60611

Northwestern University Memorial Hospital, Chicago

66160

University of Kansas Medical Center Research Institute, Inc., Kansas City

66211

Quintiles Overland Park Phase 1 Unit, Overland Park

73104

University of Oklahoma Health Sciences Center, Oklahoma City

75014

Hôpital Cochin, Paris

83712

St. Luke's Cystic Fibrosis Center of Idaho, Boise

89107

Children's Lung Specialists, Las Vegas

94305

Stanford University Medical Center, Stanford

02114

Massachusetts General Hospital, Boston

02115

Childrens Hospital Boston, Boston

V6Z 1Y6

St. Paul's Hospital Pacific Lung Research Center, Vancouver

M5B 1W8

St. Michael's Hospital, Toronto

H2X 0A9

Institut de Recherches Cliniques de Montreal, Montreal

G1V 4G5

Institut Universitaire de Cardiologie et de Pneumologie de Quebec, Québec

All Listed Sponsors
lead

Proteostasis Therapeutics, Inc.

INDUSTRY

NCT02718495 - Study Assessing PTI-428 Safety, Tolerability, and Pharmacokinetics in Subjects With Cystic Fibrosis | Biotech Hunter | Biotech Hunter