66
Participants
Start Date
January 31, 2014
Primary Completion Date
November 30, 2035
Study Completion Date
November 30, 2035
Safety and efficacy assessments
"Genetic: No interventional drug product utilized in this follow-up study~Participants received a single IV infusion of LentiGlobin BB305 Drug Product in the parent studies. Vector copy number (VCN) measurement, safety evaluations, disease-specific assessments, and assessments to monitor for long-term effects of autologous transplant are conducted in this study."
Oakland
Chicago
Bethesda
New York
Philadelphia
Charleston
Sydney
Marseille
Paris
Hanover
Heidelberg
Thessaloniki
Rome
Bangkok
London
Lead Sponsor
Genetix Biotherapeutics Inc.
INDUSTRY