131
Participants
Start Date
January 20, 2016
Primary Completion Date
December 18, 2018
Study Completion Date
December 18, 2018
Olesoxime
Participants will receive homogeneous suspension of olesoxime.
UZ Leuven Gasthuisberg, Leuven
UZ Gent, Ghent
Hopital la Timone Enfants; Service de Pediatrie et Neurologie Pediatrique, Marseille
IRCCS Istituto G. Gaslini; UOC Neurologia Pediatrica e Malattie Muscolari, Genoa
I.R.C.C.S. Cà Granda - Ospedale Maggiore Policlinico; Dip. di Salute Mentale, Milan
ASST GRANDE OSPEDALE METROPOLITANO NIGUARDA;NEMO (NEuroMuscular Omnicentre);Centro clinico - Fonda, Milan
Hopital des Enfants; Unite de Neurologie Pediatrique, Toulouse
CHRU de Montpellier, Hopital Gui de Chauliac; Service de Neuropediatrie, Montpellier
Universitätsklinikum Essen; Neuropädiatrie, Essen
Hopital Jeanne De Flandre; CIC pediatrique, Lille
Hopital Femme Mere Enfant; Medecine Physique et Readaptation Pediatrique - L'ESCALE, Bron
Hopital Armand Trousseau; centre reference Maladies Neuro-musculaires Est parisien Neuropediatrie, Paris
Uniklinikum Freiburg Zentrum für Kinder- und Jugendmedizin; Neuropädiatrie und Muskelerkrankungen, Freiburg im Breisgau
Dr. Von Haunersches Kinderspital, München
Hôpital Raymond Poincare; Serv. Neurologie et Réanimation pédiatriques - Centre réf. neuromusculaire, Garches
Azienda Ospedaliera Universitaria Policlinico G.Martino; Dip. Neurologia e Malattie neuromuscolari, Messina
Ospedale Pediatrico Bambino Gesù; Dip. Neuroscienze e Salute Mentale, Rome
Policlinico Agostino Gemelli; Dipartimento di Neuropsichiatria Infantile, Rome
UMC Utrecht; Polkliniek Neuromusculaire ziekten, Utrecht
Samodzielny Publiczny Centralny Szpital Kliniczny w Warszawie; Klinika Neurologii, Warsaw
Heart of England NHS Trust, Birmingham
National Hospital for Neurology and Neurosurgery,; MRC Centre for Neuromuscular Diseases, London
Great Ormond Street Hospital, London
Newcastle University & The Newcastle upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne
Hoffmann-La Roche
INDUSTRY