A Study to Evaluate Long Term Safety, Tolerability, and Effectiveness of Olesoxime in Patients With Spinal Muscular Atrophy (SMA)

PHASE2CompletedINTERVENTIONAL
Enrollment

131

Participants

Timeline

Start Date

January 20, 2016

Primary Completion Date

December 18, 2018

Study Completion Date

December 18, 2018

Conditions
Muscular Atrophy, Spinal
Interventions
DRUG

Olesoxime

Participants will receive homogeneous suspension of olesoxime.

Trial Locations (24)

3000

UZ Leuven Gasthuisberg, Leuven

9000

UZ Gent, Ghent

13005

Hopital la Timone Enfants; Service de Pediatrie et Neurologie Pediatrique, Marseille

16147

IRCCS Istituto G. Gaslini; UOC Neurologia Pediatrica e Malattie Muscolari, Genoa

20100

I.R.C.C.S. Cà Granda - Ospedale Maggiore Policlinico; Dip. di Salute Mentale, Milan

20162

ASST GRANDE OSPEDALE METROPOLITANO NIGUARDA;NEMO (NEuroMuscular Omnicentre);Centro clinico - Fonda, Milan

31059

Hopital des Enfants; Unite de Neurologie Pediatrique, Toulouse

34295

CHRU de Montpellier, Hopital Gui de Chauliac; Service de Neuropediatrie, Montpellier

45147

Universitätsklinikum Essen; Neuropädiatrie, Essen

59037

Hopital Jeanne De Flandre; CIC pediatrique, Lille

69677

Hopital Femme Mere Enfant; Medecine Physique et Readaptation Pediatrique - L'ESCALE, Bron

75571

Hopital Armand Trousseau; centre reference Maladies Neuro-musculaires Est parisien Neuropediatrie, Paris

79106

Uniklinikum Freiburg Zentrum für Kinder- und Jugendmedizin; Neuropädiatrie und Muskelerkrankungen, Freiburg im Breisgau

80337

Dr. Von Haunersches Kinderspital, München

92380

Hôpital Raymond Poincare; Serv. Neurologie et Réanimation pédiatriques - Centre réf. neuromusculaire, Garches

98125

Azienda Ospedaliera Universitaria Policlinico G.Martino; Dip. Neurologia e Malattie neuromuscolari, Messina

00165

Ospedale Pediatrico Bambino Gesù; Dip. Neuroscienze e Salute Mentale, Rome

00168

Policlinico Agostino Gemelli; Dipartimento di Neuropsichiatria Infantile, Rome

3584 CX

UMC Utrecht; Polkliniek Neuromusculaire ziekten, Utrecht

02-097

Samodzielny Publiczny Centralny Szpital Kliniczny w Warszawie; Klinika Neurologii, Warsaw

B9 5SS

Heart of England NHS Trust, Birmingham

WC1 3BG

National Hospital for Neurology and Neurosurgery,; MRC Centre for Neuromuscular Diseases, London

WC1N 3JH

Great Ormond Street Hospital, London

NE1 4LP

Newcastle University & The Newcastle upon Tyne Hospitals NHS Foundation Trust, Newcastle upon Tyne

All Listed Sponsors
lead

Hoffmann-La Roche

INDUSTRY

NCT02628743 - A Study to Evaluate Long Term Safety, Tolerability, and Effectiveness of Olesoxime in Patients With Spinal Muscular Atrophy (SMA) | Biotech Hunter | Biotech Hunter