Arimoclomol Prospective Study in Participants Diagnosed With Niemann-Pick Disease Type C

University Hospital Copenhagen (Rigshospitalet), Copenhagen

"Azienda Ospedaliero-Universitaria Santa Maria della Misericordia di Udin", Udine

Villa Metabolica, Universitätsmedizin Mainz, Mainz

Mayo Clinic Children's Center, Rochester

Dr. von Haunersches Kinderspital der Universität München, Munich

UCSF Benioff Children's Hospital Oakland, Oakland

CHU de Montpellier, Montpellier

Hôpital Trousseau, Paris

Ospedale Pediatrico Bambino Gesù, Rome

The Children´s Memorial Istitute Warsaw, Warsaw

Hospital Vall D'Hebron, Barcelona

INSELSPITAL University Hospital Bern, Bern

Birmingham Children's Hospital, Birmingham

Great Ormond Street Hospital, London