Study of Cavosonstat (N91115) in Patients With CF Homozygous for the F508del-CFTR Mutation

PHASE2CompletedINTERVENTIONAL
Enrollment

138

Participants

Timeline

Start Date

November 30, 2015

Primary Completion Date

December 31, 2016

Study Completion Date

December 31, 2016

Conditions
Cystic Fibrosis
Interventions
DRUG

Cavosonstat

GSNOR inhibitor

DRUG

Placebo

Control sample with only capsule excipients and fillers

Trial Locations (46)

10032

Columbia University, New York

15224

Children's Hospital of Pittsburgh of UPMC, Pittsburgh

19104

Children's Hospital of Philadelphia, Philadelphia

21287

Johns Hopkins Hospital, Baltimore

27103

Wake Forest University School of Medicine, Winston-Salem

27599

University of North Carolina Chapel Hill, Chapel Hill

29425

Medical University of South Carolina, Charleston

33606

Tampa General Hospital, Tampa

35294

University of Alabama, Birmingham

40536

University of Kentucky, Lexington

43205

Nationwide Children's Hospital, Columbus

43606

ProMedica Toledo Children's Hospital, Toledo

44106

Rainbow Babies and Children's Hospital - Case Medical Center, Cleveland

44308

Children's Hospital Medical Center of Akron, Akron

45229

Cincinnati Children's Hospital, Cincinnati

46202

Indiana University, Indianapolis

48202

Wayne State University-Harper, Detroit

49503

Spectrum Health Butterworth Hospital, Grand Rapids

52242

University of Iowa Children's Hospital, Iowa City

53792

Medical Center of Wisconsin, Madison

55455

University of Minnesota, Minneapolis

60611

Northwestern University, Chicago

61637

Saint Francis Medical Center, Peoria

63104

St. Louis University, St Louis

63110

Washington University, St Louis

67214

Via Christi Research, Wichita

68198

University of Nebraska Medical Center, Omaha

75390

University of Texas Southwestern Medical Center, Dallas

76104

Cook Children's Medical Center, Fort Worth

77030

Texas Children's Hospital, Houston

80045

Children's Hospital Colorado, Aurora

80206

National Jewish Health, Denver

83712

St. Luke's CF Center of Idaho, Boise

84132

University of Utah, Salt Lake City

85724

Banner University of Arizona Medical Center, Tucson

90027

Children's Hospital Los Angeles, Los Angeles

94304

Stanford University, Palo Alto

95817

UC Davis Medical Center, Sacramento

97239

Oregon Health and Science University, Portland

98105

Seattle Children's Hospital, Seattle

06510

Yale University, New Haven

04102

Maine Medical Center, Portland

02115

Boston Children's Hospital, Boston

01655

University of Massachusetts Medical School, Worcester

07960

Morristown Medical Center, Morristown

Texas

"Dell Children's Hospital , Austin Children's Chest Associates"

Sponsors
All Listed Sponsors
collaborator

Medidata Solutions

INDUSTRY

lead

Nivalis Therapeutics, Inc.

INDUSTRY