50
Participants
Start Date
September 30, 2015
Primary Completion Date
January 31, 2026
Study Completion Date
January 31, 2026
N-acetylcysteine
1800mg NAC twice daily (3600mg/day) orally for approximately 90 days.
RECRUITING
New York University, New York
RECRUITING
University of Minnesota, Minneapolis
Rare Diseases Clinical Research Network
NETWORK
National Center for Advancing Translational Sciences (NCATS)
NIH
National Institute of Diabetes and Digestive and Kidney Diseases (NIDDK)
NIH
National Institute of Neurological Disorders and Stroke (NINDS)
NIH
Lysosomal Disease Network
OTHER
University of Minnesota
OTHER