An Efficacy and Safety Study of AG-221 (CC-90007) Versus Conventional Care Regimens in Older Subjects With Late Stage Acute Myeloid Leukemia Harboring an Isocitrate Dehydrogenase 2 Mutation

PHASE3CompletedINTERVENTIONAL
Enrollment

319

Participants

Timeline

Start Date

December 30, 2015

Primary Completion Date

March 17, 2020

Study Completion Date

March 25, 2024

Conditions
Leukemia, MyeloidIsocitrate Dehydrogenase
Interventions
DRUG

AG-221

Continuous 28-day cycles of AG 221 100 mg orally (PO) once a day (QD) for 28 days

OTHER

BSC

Best supportive care includes, hydroxyurea for leukocytosis and/or differentiation-like syndrome, anti-infectives, analgesics, antiemetics, antipyretics, transfusions and nutritional support

DRUG

Azacitidine

continuous 28-day cycles of azacitidine 75 mg/m2/day SC for 7 days, plus BSC

DRUG

Low-dose cytarabine (LDAC)

continuous 28-day cycles of cytarabine 20 mg SC twice a day (BID) for 10 days, plus BSC

DRUG

Intermediate-dose cytarabine (IDAC)

28-day cycles of cytarabine 0.5 to 1.5 g/m2/day IV for 3 to 6 days, per standard institutional practice, plus BSC; only BSC given after IDAC therapy concludes per standard institutional practice

Trial Locations (93)

0

Local Institution - 889, Zhengzhou

333

Local Institution - 941, Taoyuan District

404

Local Institution - 942, Taichung, Northern Dist.

2100

Local Institution - 831, Copenhagen

2139

Local Institution - 901, Concord

3002

Local Institution - 906, East Melbourne

3004

Local Institution - 905, Melbourne

4020

Local Institution - 803, Linz

5000

Local Institution - 904, Adelaide

5530

Local Institution - 811, Yvoir

6500

Local Institution - 871, Ankara

8036

Local Institution - 704, Barcelona

10002

Local Institution - 940, Taipei, Zhongzheng Dist.

10029

Local Institution - 128, New York

10467

Montefiore Medical Center Albert Einstein Cancer Center, The Bronx

13273

Local Institution - 612, Marseille

14263

Roswell Park Cancer Institute, Buffalo

14642

Strong Health System, Rochester

20070

Local Institution - 874, Denizli

25123

Local Institution - 304, Brescia

27310

Local Institution - 875, Gaziantep

27705

Duke University Medical Center, Durham

29615

Local Institution - 104, Greenville

30625

Local Institution - 401, Hanover

31009

Local Institution - 609, Toulouse

32806

University of Florida Health Cancer Center at Orlando Health, Orlando

33011

Local Institution - 701, Oviedo

33136

Local Institution - 121, Miami

33604

Local Institution - 607, Pessac

37007

Local Institution - 709, Salamanca

40138

Local Institution - 305, Bologna

41013

Local Institution - 702, Seville

44093

Local Institution - 601, Nantes

44106

University Hospitals Cleveland Medical Center, Cleveland

45122

Local Institution - 413, Essen

46009

Local Institution - 706, Avda, Campanar 21

49033

Local Institution - 606, Angers

50139

Local Institution - 302, Florence

55131

Local Institution - 402, Mainz

59037

Local Institution - 602, Lille

60590

Local Institution - 406, Frankfurt

60637

Local Institution - 111, Chicago

69495

Local Institution - 611, Pierre-Bénite

75246

Baylor Sammons Cancer Center, Dallas

78000

Local Institution - 610, Versailles

80131

Local Institution - 301, Naples

81377

Local Institution - 409, München

89081

Local Institution - 407, Ulm

89100

Local Institution - 303, Reggio Calabria

90146

Local Institution - 306, Palermo

93009

Local Institution - 605, Bobigny

94805

Local Institution - 604, Villejuif

100080

Local Institution - 885, Beijing

100191

Local Institution - 884, Beijing

100853

Local Institution - 892, Beijing

123182

Local Institution - 864, Moscow

129301

Local Institution - 863, Moscow

191024

Local Institution - 862, Saint Petersburg

200025

Local Institution - 887, Shanghai

200433

Local Institution - 891, Shanghai

310006

Local Institution - 883, Hangzhou

350001

Local Institution - 882, Fuzhou

510080

Local Institution - 881, Guangzhou, Guangdong

610041

Local Institution - 888, Chengdu, Sichuan

660022

Local Institution - 861, Krasnoyarsk

07601

John Theurer Cancer Center at Hackensack University Medical Center, Hackensack

90020-090

Local Institution - 250, Porto Alegre

90035-003

Local Institution - 252, Porto Alegre, RS

17210-080

Local Institution - 251, Jaú

20211-030

Local Institution - 253, Rio de Janeiro

01308-050

Local Institution - 254, São Paulo

T6G2V2

Local Institution - 202, Edmonton

R3E OV9

Local Institution - 203, Winnipeg

M5G 2M9

Local Institution - 201, Toronto

H3A 1A1

Local Institution - 204, Montreal

128 08

Local Institution - 822, Prague

DK-9000

Local Institution - 834, Aalborg

DK-8000

Local Institution - 833, Arhus C

DK-5000

Local Institution - 832, Odense

D-01307

Local Institution - 403, Dresden

04103

Local Institution - 412, Leipzig

00133

Local Institution - 307, Roma

519-809

Local Institution - 953, Hwasun-gun

137-701

Local Institution - 952, Seoul

08035

Local Institution - 708, Barcelona

06100

Local Institution - 873, Ankara

06200

Local Institution - 872, Ankara

NG5 1PB

Local Institution - 503, Nottingham

EC1A 7BE

Local Institution - 501, London

SE5 9RS

Local Institution - 507, London

M20 4BX

Local Institution - 502, Manchester Withington

OX3 9DU

Local Institution - 510, Oxford

SM2 5PT

Local Institution - 509, Sutton (Surrey)

Sponsors

Lead Sponsor

All Listed Sponsors
lead

Celgene

INDUSTRY