Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases

CompletedOBSERVATIONAL
Enrollment

230

Participants

Timeline

Start Date

June 30, 2015

Primary Completion Date

December 18, 2024

Study Completion Date

December 18, 2024

Conditions
Spinal Muscular AtrophyCharcot-Marie-Tooth DiseaseMuscular DystrophySpinal Muscular Atrophy With Respiratory Distress 1Amyotrophic Lateral SclerosisMotor Neuron DiseaseNeuromuscular DiseasePeroneal Muscular Atrophy
Interventions
OTHER

sample collection

collection of blood

Trial Locations (3)

19803

Nemours Children's Hospital Delaware, Wilmington

32207

Nemours Children's Specialty Care, Jacksonville

32827

Nemours Children's Hospital Orlando, Orlando

All Listed Sponsors
lead

Nemours Children's Clinic

OTHER

NCT02532244 - Genetics of Pediatric-Onset Motor Neuron and Neuromuscular Diseases | Biotech Hunter | Biotech Hunter