Study of SRP-4045 (Casimersen) and SRP-4053 (Golodirsen) in Participants With Duchenne Muscular Dystrophy (DMD)

PHASE3Active, not recruitingINTERVENTIONAL
Enrollment

228

Participants

Timeline

Start Date

September 28, 2016

Primary Completion Date

November 12, 2024

Study Completion Date

October 17, 2025

Conditions
Duchenne Muscular Dystrophy
Interventions
DRUG

SRP-4045

SRP-4045 solution for IV infusion

DRUG

SRP-4053

SRP-4053 solution for IV infusion

DRUG

Placebo

SRP-4045 or SRP-4053 placebo-matching solution for IV infusion

Trial Locations (75)

1083

Semmelweis Egyetem Genomikai Medicina és Ritka Betegsegek Intezete, Budapest

1111

DOM Centro de Reumatologia, Buenos Aires

1431

University Multiprofile Hospital for Active Treatment Aleksandrovska EAD, Sofia

2100

Rigshospitalet Copenhagen University Hospital, København Ø

2145

Children's Hospital at Westmead, Westmead

3000

Universitair Ziekenhuis Leuven, Leuven

3052

Royal Children's Hospital Melbourne, Parkville

4000

CHR de la Citadelle, Liège

4101

Queensland Children's Hospital, South Brisbane

9000

Universitair Ziekenhuis Gent, Ghent

11000

Clinic for Neurology and Psychiatry for Children and Youth, Belgrade

13353

Charité - Universitätsmedizin Berlin, Berlin

14642

University of Rochester Clinical Research Center, Rochester

15008

Fakultni nemocnice v Motole, Prague

15123

IASO Children's Hospital, Marousi

15224

Children's Hospital of Pittsburgh of UPMC, Pittsburgh

16147

Istituto Giannina Gaslini, Genoa

20133

Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan

23507

Children's Hospital of the King's Daughters, Norfolk

30318

Center for Integrative Rare Disease Research (CIRDR), Atlanta

31059

Hôpital Des Enfants, Toulouse

32561

NW Florida Clinical Research Group, LLC, Gulf Breeze

32610

University of Florida, Gainesville

34000

Instituto de Investigaciones Clínicas para la Salud A.C, Durango

43205

Nationwide Children's Hospital, Columbus

44093

Reference Centre for Neuromuscular Diseases, Nantes

44124

Azienda Ospedaliero-Universitaria di Ferrara - Arcispedale Sant' Anna, Ferrara

45122

Universitätsklinikum Essen, Essen

45229

Cincinnati Children's Hospital Medical Center (CCHMC), Cincinnati

49102

Schneider Children's Medical Center of Israel, Petah Tikvah

50612

Pusan National University Yangsan Hospital, Yangsan

52242

University of Iowa Children's Hospital, Iowa City

53226

Children's Hospital of Wisconsin, Milwaukee

54642

Ippokratio General Hospital of Thessaloniki, Thessaloniki

60611

Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago

61300

University Hospital Brno, Brno

63110

St. Louis Children's Hospital, St Louis

66160

University of Kansas, Medical Center, Kansas City

75012

Hôpital Armand Trousseau, Paris

75235

Children's Medical Center Dallas, Dallas

79106

University Hospital Freiburg, Freiburg im Breisgau

80020

Neurociencias Estudios Clínicos S.C, Culiacán

84132

University of Utah, Salt Lake City

85028

Neuromuscular Research Center, Phoenix

89145

Las Vegas Clinic, Las Vegas

90027

Children's Hospital Los Angeles, Los Angeles

90095

David Geffen School of Medicine, UCLA, Los Angeles

92123

Rady Children's Hospital San Diego/ UCSD, San Diego

94305

Stanford University School of Medicine/Medical Center, Stanford

97239

Shriners Hospital for Children, Portland

98125

Az Ospedaliera Universitaria Policlinico G Martino, Messina

125412

"Federal state budget educational institution of higher education Russian national research medical university n.a. N.I. Pirogov of Ministry of healthcare of Russian Federation", Moscow

380054

Royal Instituite of Child Neurosciences, Ahmedabad

411004

Deenanth Mangeshkar Hospital, Pune

02115

Boston Children's Hospital, Boston

T3B 6A8

Alberta Childrens Hospital, Calgary

V6H 3V4

Children's and Women's Health Centre of British Columbia, Vancouver

N6A 5W9

London Health Sciences Centre, London

K1H 8L1

Children's Hospital of Eastern Ontario, Ottawa

D1

The Children's University Hospital, Dublin

00168

Policlinico Universitario A Gemelli, Rome

02-097

Samodzielny Publiczny Centralny Szpital Kliniczny, Warsaw

80-952

Uniwersyteckie Centrum Kliniczne, Gdansk

Unknown

State Autonomous Healthcare Institution of Sverdlovsk Region Children's Clinical Hospital No. 9 City of Ekaterinburg, Yekaterinburg

Hospital Universitari i Politecnic La Fe de Valencia, Valencia

03080

Seoul National University Hospital, Seoul

08041

Hospital de La Santa Creu i Sant Pau, Barcelona

08950

Hospital Sant Joan de Deu, Barcelona

SE-41685

Drottning Silvias Barn Och Ungdomssjukhus, Gothenburg

G51 4TF

Royal Hospital for Children (Glasgow), Glasgow

LS1 3EX

Leeds Teaching Hospitals NHS Trust, Leeds

L12 2AP

Alder Hey Childrens Hospital, Liverpool

WC1N 1EH

Great Ormond Street Hospital (GOSH), London

NE1 4LP

Royal Victoria Infirmary, Newcastle upon Tyne

OX3 9DU

John Radcliffe Hospital, Oxford

All Listed Sponsors
lead

Sarepta Therapeutics, Inc.

INDUSTRY