228
Participants
Start Date
September 28, 2016
Primary Completion Date
November 12, 2024
Study Completion Date
October 17, 2025
SRP-4045
SRP-4045 solution for IV infusion
SRP-4053
SRP-4053 solution for IV infusion
Placebo
SRP-4045 or SRP-4053 placebo-matching solution for IV infusion
Semmelweis Egyetem Genomikai Medicina és Ritka Betegsegek Intezete, Budapest
DOM Centro de Reumatologia, Buenos Aires
University Multiprofile Hospital for Active Treatment Aleksandrovska EAD, Sofia
Rigshospitalet Copenhagen University Hospital, København Ø
Children's Hospital at Westmead, Westmead
Universitair Ziekenhuis Leuven, Leuven
Royal Children's Hospital Melbourne, Parkville
CHR de la Citadelle, Liège
Queensland Children's Hospital, South Brisbane
Universitair Ziekenhuis Gent, Ghent
Clinic for Neurology and Psychiatry for Children and Youth, Belgrade
Charité - Universitätsmedizin Berlin, Berlin
University of Rochester Clinical Research Center, Rochester
Fakultni nemocnice v Motole, Prague
IASO Children's Hospital, Marousi
Children's Hospital of Pittsburgh of UPMC, Pittsburgh
Istituto Giannina Gaslini, Genoa
Fondazione IRCCS Istituto Neurologico Carlo Besta, Milan
Children's Hospital of the King's Daughters, Norfolk
Center for Integrative Rare Disease Research (CIRDR), Atlanta
Hôpital Des Enfants, Toulouse
NW Florida Clinical Research Group, LLC, Gulf Breeze
University of Florida, Gainesville
Instituto de Investigaciones Clínicas para la Salud A.C, Durango
Nationwide Children's Hospital, Columbus
Reference Centre for Neuromuscular Diseases, Nantes
Azienda Ospedaliero-Universitaria di Ferrara - Arcispedale Sant' Anna, Ferrara
Universitätsklinikum Essen, Essen
Cincinnati Children's Hospital Medical Center (CCHMC), Cincinnati
Schneider Children's Medical Center of Israel, Petah Tikvah
Pusan National University Yangsan Hospital, Yangsan
University of Iowa Children's Hospital, Iowa City
Children's Hospital of Wisconsin, Milwaukee
Ippokratio General Hospital of Thessaloniki, Thessaloniki
Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago
University Hospital Brno, Brno
St. Louis Children's Hospital, St Louis
University of Kansas, Medical Center, Kansas City
Hôpital Armand Trousseau, Paris
Children's Medical Center Dallas, Dallas
University Hospital Freiburg, Freiburg im Breisgau
Neurociencias Estudios Clínicos S.C, Culiacán
University of Utah, Salt Lake City
Neuromuscular Research Center, Phoenix
Las Vegas Clinic, Las Vegas
Children's Hospital Los Angeles, Los Angeles
David Geffen School of Medicine, UCLA, Los Angeles
Rady Children's Hospital San Diego/ UCSD, San Diego
Stanford University School of Medicine/Medical Center, Stanford
Shriners Hospital for Children, Portland
Az Ospedaliera Universitaria Policlinico G Martino, Messina
"Federal state budget educational institution of higher education Russian national research medical university n.a. N.I. Pirogov of Ministry of healthcare of Russian Federation", Moscow
Royal Instituite of Child Neurosciences, Ahmedabad
Deenanth Mangeshkar Hospital, Pune
Boston Children's Hospital, Boston
Alberta Childrens Hospital, Calgary
Children's and Women's Health Centre of British Columbia, Vancouver
London Health Sciences Centre, London
Children's Hospital of Eastern Ontario, Ottawa
The Children's University Hospital, Dublin
Policlinico Universitario A Gemelli, Rome
Samodzielny Publiczny Centralny Szpital Kliniczny, Warsaw
Uniwersyteckie Centrum Kliniczne, Gdansk
State Autonomous Healthcare Institution of Sverdlovsk Region Children's Clinical Hospital No. 9 City of Ekaterinburg, Yekaterinburg
Hospital Universitari i Politecnic La Fe de Valencia, Valencia
Seoul National University Hospital, Seoul
Hospital de La Santa Creu i Sant Pau, Barcelona
Hospital Sant Joan de Deu, Barcelona
Drottning Silvias Barn Och Ungdomssjukhus, Gothenburg
Royal Hospital for Children (Glasgow), Glasgow
Leeds Teaching Hospitals NHS Trust, Leeds
Alder Hey Childrens Hospital, Liverpool
Great Ormond Street Hospital (GOSH), London
Royal Victoria Infirmary, Newcastle upon Tyne
John Radcliffe Hospital, Oxford
Sarepta Therapeutics, Inc.
INDUSTRY