A Study of Mucopolysaccharidosis Type IIIB (MPS IIIB)

CompletedOBSERVATIONAL
Enrollment

22

Participants

Timeline

Start Date

November 30, 2015

Primary Completion Date

April 30, 2019

Study Completion Date

April 30, 2019

Conditions
Mucopolysaccharidosis Type IIIBMucopolysaccharidosis Type 3 BMPS III BMPS 3 B
Trial Locations (8)

94609

Children's Hospital and Research Center Oakland, Oakland

Unknown

Melbourne Children's Trials Centre, Melbourne

Fundacion Cardioinfantil-Instituto de Cardiologia, Bogotá

University Medical Center Hamburg Eppendorf, Department of Pediatrics, Hamburg

Hospital Clinico Universitario de Santiago, Santiago de Compostela

MacKay Memorial Children's Hospital, Taipei

Gazi University Faculty of Medicine, Ankara

Somers Clinical Research Facility, Great Ormond Street Hospital, London

Sponsors
All Listed Sponsors
lead

Allievex Corporation

INDUSTRY