21
Participants
Start Date
August 19, 2015
Primary Completion Date
September 24, 2018
Study Completion Date
September 24, 2018
Nusinersen
Administered by intrathecal injection.
Sham Procedure
Small needle prick on the lower back at the location where the IT injection is normally made.
The Johns Hopkins Hospital, Baltimore
Gillette Children's Specialty Healthcare, Saint Paul
The University of Texas Southwestern Medical Center, Dallas
LMU-Campus Innenstadt, München
Seattle Children's Research Institute, Seattle
David Geffen School of Medicine at UCLA, Los Angeles
Connecticut Childrens Medical, Hartford
Lead Sponsor
Biogen
INDUSTRY