500
Participants
Start Date
April 30, 2015
Primary Completion Date
December 31, 2025
Study Completion Date
December 31, 2030
RECRUITING
Cincinnati Children's Hospital Medical Center, Cincinnati
Rare Diseases Clinical Research Network
NETWORK
National Heart, Lung, and Blood Institute (NHLBI)
NIH
National Center for Advancing Translational Sciences (NCATS)
NIH
Children's Hospital Medical Center, Cincinnati
OTHER