170
Participants
Start Date
May 31, 2015
Primary Completion Date
December 31, 2025
Study Completion Date
December 31, 2026
RECRUITING
Cleveland Clinic, Cleveland
RECRUITING
Cincinnati Children's Hospital Medical Center, Cincinnati
RECRUITING
University of California at Los Angeles, Los Angeles
RECRUITING
Stanford University Medical Center, Stanford
RECRUITING
Boston Children's Hospital, Boston
National Institutes of Health (NIH)
NIH
National Institute of Neurological Disorders and Stroke (NINDS)
NIH
Office of Rare Diseases (ORD)
NIH
National Center for Advancing Translational Sciences (NCATS)
NIH
Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD)
NIH
Boston Children's Hospital
OTHER