A Prospective Non-therapeutic Study in Patients Diagnosed With Niemann-Pick Disease Type C

CompletedOBSERVATIONAL
Enrollment

35

Participants

Timeline

Start Date

September 30, 2015

Primary Completion Date

May 31, 2017

Study Completion Date

May 31, 2017

Conditions
Niemann-Pick Disease, Type C
Trial Locations (16)

2100

University Hospital Copenhagen (Rigshospitalet), Copenhagen

3010

Inselspital, University Hospital Bern, Bern

20133

Istituto Carlo Besta (Milano), Milan

20900

Azienda Ospedaliera San Gerardo, Monza

50006

Hospital Quirón, Zaragoza

55131

Villa Metabolica Mainz, Mainz

80138

Università Federico II, Napoli

Unknown

CHU de Montpellier, Montpellier

Hôpital Trousseau, Paris

Klinikum der Universistat, Munchen, Munich

"Azienda Ospedaliero-Universitaria Santa Maria della Misericordia", Udine

00146

Ospedale Pediatrico Bambino Gesù, Rome

04-730

The Children´s Memorial Istitute Warsaw, Warsaw

08035

Hospital Vall D'Hebron, Barcelona

B4 6NH

Birmingham Children's Hospital, Birmingham

WC1N 3JH

Great Ormond Street Hospital, London

All Listed Sponsors
lead

ZevraDenmark

INDUSTRY

NCT02435030 - A Prospective Non-therapeutic Study in Patients Diagnosed With Niemann-Pick Disease Type C | Biotech Hunter | Biotech Hunter