NCT02432768View on ClinicalTrials.gov

The Effect of Triheptanoin in Adults With McArdle Disease (Glycogen Storage Disease Type V)

PHASE2CompletedINTERVENTIONAL
Enrollment

22

Participants

Timeline

Start Date

April 30, 2015

Primary Completion Date

April 30, 2018

Study Completion Date

February 28, 2019

Conditions
Glycogen Storage Disease Type V
Interventions
DRUG

Triheptanoin

Anaplerotic dietary oil

OTHER

Placebo oil

Safflower oil

Trial Locations (1)

2100

Copenhagen Neuromuscular Center, 3342, Rigshospitalet, Copenhagen

All Listed Sponsors
collaborator

Groupe Hospitalier Pitie-Salpetriere

OTHER

collaborator

University of Texas Southwestern Medical Center

OTHER

collaborator

Ultragenyx Pharmaceutical Inc

INDUSTRY

lead

Rigshospitalet, Denmark

OTHER

NCT02432768 - The Effect of Triheptanoin in Adults With McArdle Disease (Glycogen Storage Disease Type V) | Biotech Hunter | Biotech Hunter