Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia

PHASE3CompletedINTERVENTIONAL
Enrollment

33

Participants

Timeline

Start Date

November 30, 2015

Primary Completion Date

March 19, 2019

Study Completion Date

March 19, 2019

Conditions
Propionic AcidemiaMethylmalonic Acidemia
Interventions
DRUG

Carglumic Acid

Carglumic Acid 50 mg/kg/day (twice daily)

Trial Locations (2)

11426

King Abdullah Specialist Children Hospital, King Abdulaziz Medical City, Riyadh

Unknown

King Fahad Medical City, Riyadh

All Listed Sponsors
lead

King Abdullah International Medical Research Center

OTHER

NCT02426775 - Carglumic Acid in Methylmalonic Acidemia and Propionic Acidemia | Biotech Hunter | Biotech Hunter