33
Participants
Start Date
November 30, 2015
Primary Completion Date
March 19, 2019
Study Completion Date
March 19, 2019
Carglumic Acid
Carglumic Acid 50 mg/kg/day (twice daily)
King Abdullah Specialist Children Hospital, King Abdulaziz Medical City, Riyadh
King Fahad Medical City, Riyadh
King Abdullah International Medical Research Center
OTHER