33
Participants
Start Date
June 30, 2015
Primary Completion Date
December 17, 2018
Study Completion Date
December 17, 2018
eteplirsen
Eteplirsen 30 mg/kg will be administered as an IV infusion once a week for 96 weeks.
Children's Hospital of Philadelphia, Philadelphia
Rare Disease Research Center, Atlanta
Children's Hospital of Atlanta, Atlanta
University of Florida, Shands Hospital, Gainesville
Nationwide Children's Hospital, Columbus
University of Iowa Children's Hospital, Iowa City
St. Louis Children's Hospital, St Louis
Neuromuscular Research Center of Arizona, Phoenix
Ronald Reagan UCLA Medical Center, Los Angeles
Stanford University Medical Center, Stanford
University of California, Davis Medical Center, Sacramento
Shriners Hospital for Children, Portland
Seattle Children's Hospital, Seattle
Sarepta Therapeutics, Inc.
INDUSTRY