10
Participants
Start Date
June 10, 2015
Primary Completion Date
April 15, 2021
Study Completion Date
April 15, 2021
AAV5-hFIX
AAV5hFIX gene therapy
uniQure Investigative Site, Copenhagen
uniQure Investigative Site, Berlin
uniQure Investigative Site, Frankfurt
uniQure Investigative Site, Amsterdam
uniQure Investigative Site, Groningen
uniQure Investigative Site, Rotterdam
uniQure Investigative Site, Utrecht
Lead Sponsor
CSL Behring
INDUSTRY