Trial of AAV5-hFIX in Severe or Moderately Severe Hemophilia B

PHASE1/PHASE2CompletedINTERVENTIONAL
Enrollment

10

Participants

Timeline

Start Date

June 10, 2015

Primary Completion Date

April 15, 2021

Study Completion Date

April 15, 2021

Conditions
Hemophilia B
Interventions
GENETIC

AAV5-hFIX

AAV5hFIX gene therapy

Trial Locations (7)

Unknown

uniQure Investigative Site, Copenhagen

uniQure Investigative Site, Berlin

uniQure Investigative Site, Frankfurt

uniQure Investigative Site, Amsterdam

uniQure Investigative Site, Groningen

uniQure Investigative Site, Rotterdam

uniQure Investigative Site, Utrecht

Sponsors

Lead Sponsor

All Listed Sponsors
lead

CSL Behring

INDUSTRY