A Study of Multiple Doses of Nusinersen (ISIS 396443) Delivered to Infants With Genetically Diagnosed and Presymptomatic Spinal Muscular Atrophy

National Taiwan University Hospital, Taipei

Ospedale Pediatrico Bambino Gesù, Rome

Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City

Hamad General Hospital, Doha

Royal Children's Hospital, Parkville

Queensland Children's Hospital, South Brisbane

Hacettepe University Medical Faculty, Ankara

Columbia University, New York

The Children's Hospital of Philadelphia, Philadelphia

Fondazione Serena Onlus - Centro Clinico Nemo, Milan

The Johns Hopkins Hospital, Baltimore

Yeditepe University Medical School Hospital, Istanbul

Nemours Children's Hospital, Orlando, Orlando

Universitaetsklinikum Freiburg, Freiburg im Breisgau

Children's Hospital Colorado, Aurora

University of Utah, Salt Lake City

David Geffen School of Medicine, Los Angeles

University of California Davis Health System, Sacramento

Seattle Children's Research Institute, Seattle

Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago

Massachusetts General Hospital, Boston