National Lysosomal Acid Lipase Deficiency Study

CompletedOBSERVATIONAL
Enrollment

810

Participants

Timeline

Start Date

January 31, 2015

Primary Completion Date

January 31, 2017

Study Completion Date

March 1, 2017

Conditions
Cholesteryl Ester Storage Disease
Trial Locations (1)

Unknown

Ankara University School of Medicine, Ankara

Sponsors
All Listed Sponsors
collaborator

Alexion Pharmaceuticals, Inc.

INDUSTRY

lead

Ankara University

OTHER