Reverse Transcriptase Inhibitors in AGS

PHASE2CompletedINTERVENTIONAL
Enrollment

11

Participants

Timeline

Start Date

September 10, 2015

Primary Completion Date

January 31, 2018

Study Completion Date

June 30, 2018

Conditions
Aicardi-Goutières Syndrome (AGS)
Interventions
DRUG

Reverse transcriptase inhibitors: Zidovudine, Lamivudine, Abacavir

Oral Solution (syrup) or Tablets

Trial Locations (1)

75015

Hôpital Necker - Enfants Malades, Paris

All Listed Sponsors
collaborator

URC-CIC Paris Descartes Necker Cochin

OTHER

lead

Assistance Publique - Hôpitaux de Paris

OTHER

NCT02363452 - Reverse Transcriptase Inhibitors in AGS | Biotech Hunter | Biotech Hunter