Treosulfan-based Versus Busulfan-based Conditioning in Paediatric Patients With Non-malignant Diseases

PHASE2CompletedINTERVENTIONAL
Enrollment

106

Participants

Timeline

Start Date

April 30, 2015

Primary Completion Date

May 7, 2020

Study Completion Date

April 30, 2023

Conditions
Primary ImmunodeficienciesInborn Errors of MetabolismHaemoglobinopathiesBone Marrow Failure Syndromes
Interventions
DRUG

Treosulfan

DRUG

Busilvex

Trial Locations (21)

10126

Ospedale Infantile Regina Margherita Torino, Turin

13353

Department of Pediatric Oncology & Hematology, Charite Berlin, Berlin

20900

Reparto Trapianti Midollo Osseo Clinica Pediatrica Universitaria Fondazione MBBM-Ospedale San Gerardo, Monza

27100

S.C. Oncoematologia Pediatrica Fondazione IRCCS Policlinico San Matteo, Pavia

37134

"U.O.C. Oncoematologia Pediatrica Policlinico G.B. Rossi - AOUI Verona", Verona

45122

University Children's Hospital Essen Pediatric stem cell transplantation, Essen

56100

U.O. Oncoematologia Pediatrica Azienda Ospedaliero Universitaria Pisana Ospedale S. Chiara, Pisa

60590

University Hospital Frankfurt, Frankfurt am Main

69120

Heidelberg University Hospital, Heidelberg

89075

Ulm, University Hospital, Clinic for Children and Adolescents, Ulm

95123

UOC Ematologia ed Oncologia Pediatrica con TMO AOU Policlinico Vittorio Emanuele, Catania

Unknown

University Hospital Motol, Dep. of Paediatric Haematology and Oncology, Prague

Hannover Medical University, Dep. of Paediatrics, Paediatric Haematology and Oncology, Hanover

07747

University of Jena, Department of Pediatrics, Jena

09121

"SC Oncoematologia Pediatrica Ospedale Pediatrico Microcitemico Antonio Cao A.O. Brotzu", Cagliari

06156

Oncoematologia Pediatrica A.O. di Perugia Ospedale S. Maria della Misericordia, Perugia

00165

Ospedale Bambino Gesu Roma, Rome

85-094

Szpital Uniwersytecki im. dr Antoniego Jurasza, Bydgoszcz

30-663

Uniwersytecki Szpital Dzieciecy w Krakowie, Krakow

20-093

Dzieciecy Szpital Kliniczny im. A. Gebali w Lublinie, Lublin

50-368

Wroclaw Medical University, Department of Pediatric Hematology/Oncology and BMT, Wroclaw

All Listed Sponsors
collaborator

Celerion

INDUSTRY

collaborator

Venn Life Sciences

OTHER

collaborator

Syneos Health

OTHER

lead

medac GmbH

INDUSTRY