A Multicenter, Multinational, Observational Morquio A Registry Study (MARS)

CompletedOBSERVATIONAL
Enrollment

418

Participants

Timeline

Start Date

September 30, 2014

Primary Completion Date

February 21, 2024

Study Completion Date

February 21, 2024

Conditions
Mucopolysaccharidosis IV Type AMorquio A SyndromeMPS IVA
Interventions
DRUG

Vimizim® (elosulfase alfa)

Recombinant human N acetylgalactosamine 6 sulfatase (rhGALNS)

Trial Locations (79)

1090

Medical University of Vienna, Vienna

2145

Children's Hospital of Westmead, Westmead

2650

Antwerp University Hospital, Edegem

3052

Royal Children's Hospital - Victoria, Parkville

4101

Children's Health Queensland Hospital and Health Service, South Brisbane

5000

Royal Adelaide Hospital, Adelaide

6009

Perth Children's Hospital, Perth

6847

Royal Perth Hospital, Perth

8036

Universitätsklinik Graz, Graz

10016

NYU-Langone Medical Center School of Medicine, New York

10050

National Taiwan University Hospital, Taipei

10449

MacKay Memorial Hospital, Taipei

11217

Taipei Veterans General Hospital, Taipei

12000

Klinika Dětského a Dorostového Lékařstvi, Prague

15224

Children's Hospital of Pittsburgh of UPMC, Pittsburgh

19104

Children's Hospital of Philadelphia, Philadelphia

19803

A.I. Dupont Hospital for Children, Wilmington

20010

Children's National Health System, Washington D.C.

20090

Azienda Ospedaliero San Gerardo di Monza, Monza

23507

Children's Hospital of the King's Daughters, Norfolk

27710

Duke University Medical Center, Durham

30033

Emory University, Decatur

33155

Miami Children's Hospital, Miami

33305

Chang Gung Memorial Hospital, Taoyuan

40202

University of Louisville Research Foundation Inc. - Kosair Charities Pediatric Clinical Research Unit, Louisville

40402

China Medical University and Hospital, Taichung

40705

Taichung Veterans General Hospital, Taichung

48109

University of Michigan, Ann Arbor

50006

Changhua Christian Hospital (CCH), Changhua

50139

Azienda Ospedaliero Meyer, Florence

50586

Hospital Kuala Lumpur, Kuala Lumpur

52524

University Of Iowa, Iowa City

53226

Children's Hospital of Wisconsin, Milwaukee

54500

Hopital d'enfants - Hopitaux de Brabois, Vandœuvre-lès-Nancy

55404

Children's Hospitals and Clinics of Minnesota, Minneapolis

60611

Ann & Robert H. Lurie Children's Hospital, Chicago

69677

Hôpital Femme Mère Enfant, Bron

70403

National Cheng Kung University (NCKU) Hospital, Tainan City

72202

Arkansas Children's Hospital, Little Rock

75743

Hospital Necker, Paris

77030

UTHealth McGovern Medical School, Houston

80131

Federico II University Hospital, Naples

80756

Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City

81362

Kaohsiung Veterans General Hospital, Kaohsiung City

83301

Chang Gung Memorial Hospital Kaohsiung Branch, Kaohsiung City

85016

Phoenix Children's Hospital, Phoenix

89109

Children's Specialty Center of Nevada, Las Vegas

90027

Children's Hospital of Los Angeles, Los Angeles

90033

University of Southern California, Los Angeles

92868

Children's Hospital of Orange County, Orange

95125

Azienda Policlinico Vittorio Emanuele, presidio G Rodolico, Università di Catania, Catania

96826

Kapiolani Medical Center for Women and Children, Honolulu

02115

Children's Hospital of Boston, Boston

07960

Atlantic Health System, Morristown

98145-5005

Seattle Children's Hospital, Seattle

Unknown

Westmead Hospital, Westmead

Copenhagen University Hospital, Klinik For Sjaeldne Handicap, Copenhagen

Temple Street Children's University Hospital, Dublin

University of Malay Medical Center, Kuala Lumpur

Centro Hospitalar Lisboa Norte, Lisbon

V5Z 1M9

Adult Metabolic Diseases Clinic Vancouver General Hospital, Vancouver

V6H 3N1

Children's & Women's Centre of British Columbia, Vancouver

H3T 1C5

Sainte-Justine Hospital, Montreal

H4A 3J1

McGill University Health Centre, Montreal

J1H 5N4

Université de Sherbrooke, Sherbrooke

1105 AZ

Academic Medical Center - University of Amsterdam, Amsterdam

3015 GE

Rotterdam University Hospital Medical Centre, Rotterdam

04-730

The Children Memorial Health Institute, Warsaw

3000-062

Hospital Pediátrico de Coimbra (Centro Hospitalar de Coimbra), Coimbra

1169-045

Centro Hospitalar Lisboa Centro - Hospital de Dona Estefânia, Lisbon

00912

San Jorge Children's Hospital, Centro de Investigaciones Clinicas, San Juan

BT9 7AB

Belfast City Hospital, Belfast

B15 2WB

University Hospital Birmingham - Selly Oaks, Birmingham

B4 6NH

Birmingham Children's Hospital, Birmingham

NW3 2QG

Royal Free NHS Foundation Trust, London

WC1N 3BG

National Hospital for Neurology and Neurosurgery, London

WC1N 3JH

Great Ormond Street Hospital NHS Foundation Trust, London

M13 9WL

Royal Manchester Children's Hospital - Manchester University NHS Foundation Trust, Manchester

M6 8HD

Salford Royal NHS Foundation Trust, Salford

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

ICON plc

INDUSTRY

lead

BioMarin Pharmaceutical

INDUSTRY