418
Participants
Start Date
September 30, 2014
Primary Completion Date
February 21, 2024
Study Completion Date
February 21, 2024
Vimizim® (elosulfase alfa)
Recombinant human N acetylgalactosamine 6 sulfatase (rhGALNS)
Medical University of Vienna, Vienna
Children's Hospital of Westmead, Westmead
Antwerp University Hospital, Edegem
Royal Children's Hospital - Victoria, Parkville
Children's Health Queensland Hospital and Health Service, South Brisbane
Royal Adelaide Hospital, Adelaide
Perth Children's Hospital, Perth
Royal Perth Hospital, Perth
Universitätsklinik Graz, Graz
NYU-Langone Medical Center School of Medicine, New York
National Taiwan University Hospital, Taipei
MacKay Memorial Hospital, Taipei
Taipei Veterans General Hospital, Taipei
Klinika Dětského a Dorostového Lékařstvi, Prague
Children's Hospital of Pittsburgh of UPMC, Pittsburgh
Children's Hospital of Philadelphia, Philadelphia
A.I. Dupont Hospital for Children, Wilmington
Children's National Health System, Washington D.C.
Azienda Ospedaliero San Gerardo di Monza, Monza
Children's Hospital of the King's Daughters, Norfolk
Duke University Medical Center, Durham
Emory University, Decatur
Miami Children's Hospital, Miami
Chang Gung Memorial Hospital, Taoyuan
University of Louisville Research Foundation Inc. - Kosair Charities Pediatric Clinical Research Unit, Louisville
China Medical University and Hospital, Taichung
Taichung Veterans General Hospital, Taichung
University of Michigan, Ann Arbor
Changhua Christian Hospital (CCH), Changhua
Azienda Ospedaliero Meyer, Florence
Hospital Kuala Lumpur, Kuala Lumpur
University Of Iowa, Iowa City
Children's Hospital of Wisconsin, Milwaukee
Hopital d'enfants - Hopitaux de Brabois, Vandœuvre-lès-Nancy
Children's Hospitals and Clinics of Minnesota, Minneapolis
Ann & Robert H. Lurie Children's Hospital, Chicago
Hôpital Femme Mère Enfant, Bron
National Cheng Kung University (NCKU) Hospital, Tainan City
Arkansas Children's Hospital, Little Rock
Hospital Necker, Paris
UTHealth McGovern Medical School, Houston
Federico II University Hospital, Naples
Kaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City
Kaohsiung Veterans General Hospital, Kaohsiung City
Chang Gung Memorial Hospital Kaohsiung Branch, Kaohsiung City
Phoenix Children's Hospital, Phoenix
Children's Specialty Center of Nevada, Las Vegas
Children's Hospital of Los Angeles, Los Angeles
University of Southern California, Los Angeles
Children's Hospital of Orange County, Orange
Azienda Policlinico Vittorio Emanuele, presidio G Rodolico, Università di Catania, Catania
Kapiolani Medical Center for Women and Children, Honolulu
Children's Hospital of Boston, Boston
Atlantic Health System, Morristown
Seattle Children's Hospital, Seattle
Westmead Hospital, Westmead
Copenhagen University Hospital, Klinik For Sjaeldne Handicap, Copenhagen
Temple Street Children's University Hospital, Dublin
University of Malay Medical Center, Kuala Lumpur
Centro Hospitalar Lisboa Norte, Lisbon
Adult Metabolic Diseases Clinic Vancouver General Hospital, Vancouver
Children's & Women's Centre of British Columbia, Vancouver
Sainte-Justine Hospital, Montreal
McGill University Health Centre, Montreal
Université de Sherbrooke, Sherbrooke
Academic Medical Center - University of Amsterdam, Amsterdam
Rotterdam University Hospital Medical Centre, Rotterdam
The Children Memorial Health Institute, Warsaw
Hospital Pediátrico de Coimbra (Centro Hospitalar de Coimbra), Coimbra
Centro Hospitalar Lisboa Centro - Hospital de Dona Estefânia, Lisbon
San Jorge Children's Hospital, Centro de Investigaciones Clinicas, San Juan
Belfast City Hospital, Belfast
University Hospital Birmingham - Selly Oaks, Birmingham
Birmingham Children's Hospital, Birmingham
Royal Free NHS Foundation Trust, London
National Hospital for Neurology and Neurosurgery, London
Great Ormond Street Hospital NHS Foundation Trust, London
Royal Manchester Children's Hospital - Manchester University NHS Foundation Trust, Manchester
Salford Royal NHS Foundation Trust, Salford
Lead Sponsor
Collaborators (1)
ICON plc
INDUSTRY
BioMarin Pharmaceutical
INDUSTRY