Natural History Study to Characterise the Course of Disease Progression in Participants With Mucopolysaccharidosis Type IIIB

TerminatedOBSERVATIONAL
Enrollment

30

Participants

Timeline

Start Date

September 14, 2014

Primary Completion Date

July 11, 2017

Study Completion Date

July 11, 2017

Conditions
MPS IIIB (Sanfilippo B Syndrome)
Trial Locations (7)

Unknown

Minneapolis

Pittsburgh

Porto Alegre

Monza

Coimbra

Barcelona

Birmingham

Sponsors
All Listed Sponsors
lead

Alexion Pharmaceuticals, Inc.

INDUSTRY