NCT02254863View on ClinicalTrials.gov

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

PHASE1RecruitingINTERVENTIONAL
Enrollment

40

Participants

Timeline

Start Date

September 30, 2014

Primary Completion Date

October 31, 2026

Study Completion Date

October 31, 2026

Conditions
AdrenoleukodystrophyBatten DiseaseMucopolysaccharidosis IILeukodystrophy, Globoid CellLeukodystrophy, MetachromaticNeimann Pick DiseasePelizaeus-Merzbacher DiseaseSandhoff DiseaseTay-Sachs DiseaseBrain Diseases, Metabolic, InbornAlpha-MannosidosisSanfilippo Mucopolysaccharidoses
Interventions
BIOLOGICAL

DUOC-01

Intrathecal administration of DUOC-01

Trial Locations (1)

27705

RECRUITING

Duke University Medical Center, Durham

All Listed Sponsors
lead

Joanne Kurtzberg, MD

OTHER