30
Participants
Start Date
December 31, 2014
Primary Completion Date
September 30, 2016
Study Completion Date
September 30, 2016
Westmead Hospital, Dept. of Genetic Medicine, Westmead
Monash Medical Centre, Clayton
Women's and Children's Hospital, Adelaide
Mackay Memorial Hospital, Taipei
Hospital General Universitario Gregorio Maranon, Madrid
Hospital Universitari i Politecnic La Fe, Valencia
National University Hospital, Singapore
"Spitalul Clinic Judetean de Urgenta Sf. Apostol Andrei", Constanța
Porto Alegre
Recife
Ribeirão Preto
Alexandroupoli
Athens
Larissa
Thessaloniki
St. Vincent's University Hospital, Dublin
Belgrade
Ljubljana
Alberta Children's Hospital, Calgary
Copernicus, St. Adalbert Hospital, Gdansk
Diamond Clinic, Krakow
Insitute of Psychiatry and Neurology, Warsaw
Seoul National University Hospital, Seoul
Hospital de la Santa Creu I Sant Pau, Barcelona
Lead Sponsor
BioMarin Pharmaceutical
INDUSTRY