A Prospective, Noninterventional, Observational Study of Late-Onset Pompe Disease

TerminatedOBSERVATIONAL
Enrollment

30

Participants

Timeline

Start Date

December 31, 2014

Primary Completion Date

September 30, 2016

Study Completion Date

September 30, 2016

Conditions
Late-onset Pompe Patients Untreated or Treated With rhGAA
Trial Locations (24)

2145

Westmead Hospital, Dept. of Genetic Medicine, Westmead

3168

Monash Medical Centre, Clayton

5006

Women's and Children's Hospital, Adelaide

10449

Mackay Memorial Hospital, Taipei

28007

Hospital General Universitario Gregorio Maranon, Madrid

46026

Hospital Universitari i Politecnic La Fe, Valencia

119074

National University Hospital, Singapore

900951

"Spitalul Clinic Judetean de Urgenta Sf. Apostol Andrei", Constanța

Unknown

Porto Alegre

Recife

Ribeirão Preto

Alexandroupoli

Athens

Larissa

Thessaloniki

St. Vincent's University Hospital, Dublin

Belgrade

Ljubljana

T3B 6A8

Alberta Children's Hospital, Calgary

80-462

Copernicus, St. Adalbert Hospital, Gdansk

31-011

Diamond Clinic, Krakow

02-957

Insitute of Psychiatry and Neurology, Warsaw

110-744

Seoul National University Hospital, Seoul

08041

Hospital de la Santa Creu I Sant Pau, Barcelona

Sponsors
All Listed Sponsors
lead

BioMarin Pharmaceutical

INDUSTRY