Psychological Concomitants of Morquio A Syndrome - Longitudinal Effects of Enzyme Replacement Therapy (The MAPLE Study)

CompletedOBSERVATIONAL
Enrollment

12

Participants

Timeline

Start Date

March 31, 2014

Primary Completion Date

March 31, 2018

Study Completion Date

March 31, 2018

Conditions
Morquio A SyndromeMucopolysaccharidosis IV A
Trial Locations (1)

30033

Emory University, Decatur

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

BioMarin Pharmaceutical

INDUSTRY

lead

Nadia Ali, PhD

OTHER