59
Participants
Start Date
April 30, 2015
Primary Completion Date
December 6, 2019
Study Completion Date
December 6, 2019
Allo-HSCT
Allogeneic Hematopoietic Stem Cell Transplantation
The Children's Hospital of Philadelphia, Philadelphia
Duke University Medical Center, Durham
University of Minnesota, Minneapolis
Children's Hospital Los Angeles, Los Angeles
Stanford University, Palo Alto
Boston Children's Hospital/Massachusetts General Hospital, Boston
Hospital Austral, Buenos Aires
University Hospital Leipzig, Leipzig
Princess Maxima Center for Pediatric Oncology (PMC), Utrecht
Great Ormond Street Hospital, London
McGill University Health Centre, Montreal
IRCCS Ospedale Pediatrico Bambine Gesú, Roma
Central Manchester University Hospitals NHS Foundation Trust, Manchester
Lead Sponsor
Genetix Biotherapeutics Inc.
INDUSTRY