122
Participants
Start Date
August 19, 2014
Primary Completion Date
November 21, 2016
Study Completion Date
November 21, 2016
nusinersen
Administered by intrathecal (IT) injection as specified in the treatment arm.
Sham procedure
Small needle prick on the lower back at the location where the IT injection is normally made
Sydney Children's Hospital, Sydney
Royal Children's Hospital, Children's Neuroscience Centre, Parkville
Columbia University Medical Center, New York
Istituto Giannina Gaslini, Centro Traslazionale di Miologia e Patologie Neurodegenerative, Genova
Children's Hospital of Philadelphia - Neurology, Philadelphia
Duke Children's Hospital, Durham
Hospital Universitario La Paz, Pediatric Neurology Department, Madrid
Nemours Children's Hospital, Orlando
Universitatsklinikum Essen, Essen
Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago
Washington University School of Medicine, St Louis
Institut de Myologie, Paris
UT Southwestern Medical Center/Children's Medical Center Dallas, Dallas
Universtatsklinikum Freiburg, Zentrum fur Kinder-und Jugendmedizin , Abteilung Neuropadiatrie und Muskelerkrankungen, Freiburg im Breisgau
Children's Hospital Colorado, Aurora
Primary Children's Medical Center (University of Utah), Salt Lake City
UCLA Medical Center, Los Angeles
Doernbecher Children's Hospital, Portland
Boston Children's Hospital, Boston
Hôpital Universitaire des Enfants Reine FABIOLA (HUDERF), Brussels
British Columbia Children's Hospital/UBC, Vancouver
Hospital for Sick Children, Toronto
Pediatric Neurology Unit, Catholic University, Rome
Hyogo College of Medicine, Nishinomiya
Tokyo Women's Medical University, Tokyo
Seoul National University Hospital, Seoul
University of Gothenburg, The Queen Silvia Children's Hospital, Gothenburg
Hospital Universitario Vall d'Hebron, Barcelona
Hacettepe Children's Hospital, Ankara
UCL Institute of Child Health/Great Ormond Street, London
MRC Centre for Neuromuscular Diseases at Newcastle, Institute of Genetic Medicine Newcastle University, Newcastle
Lead Sponsor
Biogen
INDUSTRY