279
Participants
Start Date
August 31, 2014
Primary Completion Date
November 30, 2016
Study Completion Date
November 30, 2016
Ataluren (PTC124®)
Oral Ataluren TID
Placebo
Oral Placebo TID
Hôpital Universitaire des Enfants Reine Fabiola, Brussels
University Hospital Brussels, Brussels
Hospital de Niños Superiora Sor Maria Ludovica, La Plata
Hagaziekenhuis, The Hague
University Hospital Leuven, Leuven
Prince Charles Hospital, Chermside
Royal Adelaide Hospital, Adelaide
Princess Margaret Hospital, Perth
Beth Israel Medical Center, New York
New York University Langone Medical Center, New York
Columbia University Medical Center, New York
SUNY Upstate Medical University, Syracuse
Charité Universitätsmedizin Berlin, Berlin
Penn State Milton S. Hershey Medical Center, Hershey
Children's Hospital of Philadelphia, Philadelphia
Drexel University College of Medicine, Philadelphia
Lombardia Cystic Fibrosis Center, Milan
Centre de Perharidy, Roscoff
Meyer Children's Hospital, Haifa
Nemours Children's Clinic, Jacksonville
University of Miami, Miami
Miami Children's Hospital, Miami
All Children's Hospital, St. Petersburg
Hôpital Arnaud de Villeneuve, Montpellier
University of Alabama at Birmingham, Birmingham
Pulmonary Associates of Mobile PC, Mobile
University of Verona, Verona
Rainbow Babies & Children's Hospital, Cleveland
St. Josef Hospital GmbH, Bochum
University of Cincinnati, Cincinnati
Indiana University, Indianapolis
Azienda Ospedaliera A Meyer, Florence
Universitätsklinikum Köln, Cologne
Childrens Hospital of Wisconsin, Milwaukee
Ospedali Riuniti di Ancona, Ancona
Christiane Herzog CF-Zentrum, Frankfurt am Main
Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago
Washington University, St Louis
Hôpital Femme-Mère-Enfant, Bron
Santiago Reyes, MD, Oklahoma City
Hôpital Necker-Enfants Malades, Paris
University of Texas Health Science Center, Tyler
Texas Children's Hospital, Houston
Children's Hospital Colorado, Aurora
LMU Klinikum der Universität München, München
Dr. Von Haunersches Kinderspital, München
Children's Hospital Los Angeles, Los Angeles
Miller Children's Hospital Long Beach, Long Beach
Hadassah University Hospital, Jerusalem
Stanford University-Children's Hospital, Palo Alto
Children's Hospital and Research Center at Oakland, Oakland
Centre Hospitalier Regional Sud Reunion, Saint-Pierre
Children's Hospital Boston, Boston
Monmouth Medical Center, Long Branch
Morristown Medical Center, Morristown
Hospital Universitario Austral, Buenos Aires
Hospital de Niños Dr. Ricardo Gutiérrez, Buenos Aires
Hospital Sao Lucas Da Pontificia Universidade Catolica Do Rio Grande Do Sul, Porto Alegre
University Mulitiprofile Hospital for Active Treatment Sveti Georgi EAD, Plovdiv
University Multiprofile Hospital for Active Treatment Aleksandrovska EAD, Sofia
General Hospital of Thessaloniki Ippokration, Thessaloniki
Ospedale Pediatrico Bambino Gesù IRCCS, Roma
Erasmus MC, Rotterdam
Szpital Dzieciecy Polanki im Macieja Plazynskiego w Gdansku, Gdansk
Hospital Regional Universitario de Malaga, Málaga
Hospital Universitario Virgen del Rocio, Seville
Birmingham Children's Hospital NHS Foundation Trust, Birmingham
Heart of England NHS Foundation Trust, Birmingham
St James's University Hospital, Leeds
Royal Brompton Hospital, London
Southampton University Hospitals NHS Trust, Southampton
Instituto da Criança - Hospital das Clínicas, São Paulo
Clinical Research Institute of Montreal, Montreal
CHU de Quebec - Hopital CHUL, Québec
University of Toronto Hospital for Sick Children, Toronto
British Columbia Children's Hospital, Vancouver
Universitätsklinikum Jena, Jena
Azienda Policlinico Umberto I, Rome
Radboud University, Nijmegen
NZOZ Sanatorium Cassia-Villa Medica, Rabka-Zdrój
NZOZ Podkarpacki Osrodek Pulmonologii i Alergologii, Rzeszów
Instytut Matki I Dziecka, Warsaw
Hospital Universitario Vall d'Hebron, Barcelona
Hospital University, Barcelona
Hospital Sant Joan de Deu, Esplugues de Llobregat
Hospital de Sabadell, Consorci Sanitari Parc Tauli, Sabadell
Southern General Hospital, Glasgow
Llandough Hospital, Penarth
Lead Sponsor
Collaborators (1)
Cystic Fibrosis Foundation
OTHER
ECFS-Clinical Trial Network (ECFS-CTN)
UNKNOWN
PTC Therapeutics
INDUSTRY