48
Participants
Start Date
February 28, 2014
Primary Completion Date
June 26, 2017
Study Completion Date
June 26, 2017
Centre Hospitalier Regional de la Citadelle, Liège
Roger Salengro Hospital, CHU, Lille, Lille
Croix Rousse Hospital, Lyon
Hôpital Femme Mère Enfant, CHU Lyon Escale, Bron
Hôpital Armand Trousseau, Paris
Institut I-Motion, Hôpital A. Trousseau, Paris
Institut de Myologie, GH Pitié Salpêtrière, Bâtiment Babinski, Paris
Hôpital Sainte Musse, Toulon
Boston Children's Hospital, 300 Longwood Avenue, Boston
Hospital for Sick Children, 555 University Avenue, Toronto
University Hospital of Essen, Essen
Bambino Gesù Children's Hospital, Rome
Hôpital Puertas de Mar, Cadiz
Collaborators (1)
Institut de Myologie, France
OTHER
Genethon
OTHER
Valerion Therapeutics, LLC
INDUSTRY