Prospective, Longitudinal Study of the Natural History and Functional Status of Patients With Myotubular Myopathy (MTM)

CompletedOBSERVATIONAL
Enrollment

48

Participants

Timeline

Start Date

February 28, 2014

Primary Completion Date

June 26, 2017

Study Completion Date

June 26, 2017

Conditions
Myotubular Myopathy
Trial Locations (13)

4000

Centre Hospitalier Regional de la Citadelle, Liège

59000

Roger Salengro Hospital, CHU, Lille, Lille

69004

Croix Rousse Hospital, Lyon

69500

Hôpital Femme Mère Enfant, CHU Lyon Escale, Bron

75012

Hôpital Armand Trousseau, Paris

Institut I-Motion, Hôpital A. Trousseau, Paris

75651

Institut de Myologie, GH Pitié Salpêtrière, Bâtiment Babinski, Paris

83056

Hôpital Sainte Musse, Toulon

02115

Boston Children's Hospital, 300 Longwood Avenue, Boston

M5G 1X8

Hospital for Sick Children, 555 University Avenue, Toronto

D-45147

University Hospital of Essen, Essen

4-00165

Bambino Gesù Children's Hospital, Rome

21-11009

Hôpital Puertas de Mar, Cadiz

Sponsors

Collaborators (1)

All Listed Sponsors
collaborator

Institut de Myologie, France

OTHER

collaborator

Genethon

OTHER

lead

Valerion Therapeutics, LLC

INDUSTRY

NCT02057705 - Prospective, Longitudinal Study of the Natural History and Functional Status of Patients With Myotubular Myopathy (MTM) | Biotech Hunter | Biotech Hunter