NCT02053064View on ClinicalTrials.gov

Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy

PHASE1/PHASE2CompletedINTERVENTIONAL

Enrollment

4

Participants

Timeline

Start Date

May 31, 2013

Primary Completion Date

May 31, 2017

Study Completion Date

June 30, 2017

Conditions

Mucopolysaccharidosis Type III ASanfilippo Disease Type A

Interventions

GENETIC

SAF-301

Trial Locations (1)

94275

Hôpitaux Universitaires Paris Sud (Bicêtre), Le Kremlin-Bicêtre

Sponsors

Lead Sponsor

All Listed Sponsors

lead

LYSOGENE

INDUSTRY