Interferon Gamma-1b in Friedreich Ataxia (FRDA)

PHASE2CompletedINTERVENTIONAL
Enrollment

12

Participants

Timeline

Start Date

August 31, 2013

Primary Completion Date

March 31, 2014

Study Completion Date

October 31, 2014

Conditions
Friedreich Ataxia
Interventions
DRUG

Interferon Gamma-1b

"Subjects will begin by taking 10 mcg/m2 of IFN-g-1b for the first two weeks of the study. Dose will be escalated to 25 mcg/m2 of IFN-g-1b for weeks three and four of the study. Finally, the dose will be escalated to 50 mcg/m2 of IFN-g-1b for the last eight weeks of the study, which is the current dose approved by the FDA for children.~All doses will be administered via subcutaneous injection."

Trial Locations (1)

19104

Children's Hospital of Philadelphia, Philadelphia

All Listed Sponsors
collaborator

Friedreich's Ataxia Research Alliance

OTHER

collaborator

Vidara Therapeutics Research Ltd

INDUSTRY

lead

Children's Hospital of Philadelphia

OTHER

NCT01965327 - Interferon Gamma-1b in Friedreich Ataxia (FRDA) | Biotech Hunter | Biotech Hunter